Department of Psychiatry, University of Oxford, Oxford, United Kingdom; Oxford Health NHS Foundation Trust, Oxford, United Kingdom.
Graduate School of Biomedical Science, Icahn School of Medicine at Mount Sinai, New York, New York; Nash Family Department of Neuroscience, Icahn School of Medicine at Mount Sinai, New York, New York.
Biol Psychiatry. 2021 Sep 15;90(6):362-372. doi: 10.1016/j.biopsych.2021.04.008. Epub 2021 Apr 21.
A key challenge in psychiatry research is the development of high-fidelity model systems that can be experimentally manipulated to explore and test pathophysiological mechanisms of illness. In this respect, the emerging capacity to derive neural cells and circuits from human induced pluripotent stem cells (iPSCs) has generated significant excitement. This review aims to provide a critical appraisal of the potential for iPSCs in illuminating pathophysiological mechanisms in the context of other available technical approaches. We discuss the selection of iPSC phenotypes relevant to psychiatry, the information that researchers can draw on to help guide these decisions, and how researchers choose between the use of 2-dimensional cultures and the use of more complex 3-dimensional model systems. We discuss the strengths and limitations of current models and the challenges and opportunities that they present. Finally, we discuss the potential of iPSC-based model systems for clarifying the mechanisms underlying genetic risk for psychiatry and the steps that will be needed to ensure that robust and reliable conclusions can be drawn. We argue that while iPSC-based models are ideally placed to study fundamental processes occurring within and between neural cells, they are often less well suited for case-control studies, given issues relating to statistical power and the challenges in identifying which cellular phenotypes are meaningful at the level of the whole individual. Our aim is to highlight the importance of considering the hypotheses of a given study to guide decisions about which, if any, iPSC-based system is most appropriate to address it.
精神病学研究的一个关键挑战是开发能够进行实验操作的高保真模型系统,以探索和测试疾病的病理生理机制。在这方面,从人类诱导多能干细胞(iPSC)中衍生出神经细胞和回路的新兴能力引起了极大的兴趣。这篇综述旨在批判性地评估 iPSC 在阐明其他可用技术方法背景下的病理生理机制方面的潜力。我们讨论了与精神病学相关的 iPSC 表型的选择,研究人员可以利用哪些信息来帮助指导这些决策,以及研究人员如何在使用 2 维培养物和使用更复杂的 3 维模型系统之间进行选择。我们讨论了当前模型的优缺点,以及它们所带来的挑战和机遇。最后,我们讨论了基于 iPSC 的模型系统在阐明精神病学遗传风险的机制以及确保得出稳健可靠的结论所需的步骤方面的潜力。我们认为,虽然基于 iPSC 的模型非常适合研究神经细胞内和细胞间发生的基本过程,但由于与统计能力相关的问题以及在整个个体水平上确定哪些细胞表型有意义的挑战,它们通常不太适合病例对照研究。我们的目的是强调考虑给定研究的假设的重要性,以指导关于哪种(如果有的话)基于 iPSC 的系统最适合解决该研究的决策。