Department of Human Genetics, Michigan Medicine, University of Michigan, Ann Arbor, MI, USA.
The University of Michigan Neuroscience Graduate Program, Ann Arbor, MI, USA.
FEBS J. 2022 Apr;289(8):2301-2317. doi: 10.1111/febs.16196. Epub 2021 Oct 8.
Mutations in numerous chromatin regulators cause neurodevelopmental disorders (NDDs) with unknown mechanisms. Understandably, most research has focused on how chromatin regulators control gene expression that is directly relevant to brain development and function, such as synaptic genes. However, some NDD models surprisingly show ectopic expression of germline genes in the brain. These germline genes are usually expressed only in the primordial germ cells, testis, and ovaries for germ cell development and sexual reproduction. Such ectopic germline gene expression has been reported in several NDDs, including immunodeficiency, centromeric instability, facial anomalies syndrome 1; Kleefstra syndrome 1; MeCP2 duplication syndrome; and mental retardation, X-linked syndromic, Claes-Jensen type. The responsible genes, DNMT3B, G9A/GLP, MECP2, and KDM5C, all encode chromatin regulators for gene silencing. These mutations may therefore lead to germline gene derepression and, in turn, a severe identity crisis of brain cells-potentially interfering with normal brain development. Thus, the ectopic expression of germline genes is a unique hallmark defining this NDD subset and further implicates the importance of germline gene silencing during brain development. The functional impact of germline gene expression on brain development, however, remains undetermined. This perspective article explores how this apparent soma-to-germline transformation arises and how it may interfere with neurodevelopment through genomic instability and impaired sensory cilium formation. Furthermore, we also discuss how to test these hypotheses experimentally to ultimately determine the contribution of ectopic germline transcripts to chromatin-linked NDDs.
许多染色质调控因子的突变导致神经发育障碍(NDD),但其机制尚不清楚。可以理解的是,大多数研究都集中在染色质调控因子如何控制与大脑发育和功能直接相关的基因表达,如突触基因。然而,一些 NDD 模型出人意料地显示出生殖细胞基因在大脑中的异位表达。这些生殖细胞基因通常仅在原始生殖细胞、睾丸和卵巢中表达,用于生殖细胞发育和有性生殖。在几种 NDD 中,包括免疫缺陷、着丝粒不稳定、面异常综合征 1;Kleefstra 综合征 1;MeCP2 重复综合征;和智力障碍、X 连锁综合征、Claes-Jensen 型,都有报道过这种生殖细胞基因的异位表达。负责的基因,DNMT3B、G9A/GLP、MECP2 和 KDM5C,都编码基因沉默的染色质调控因子。这些突变可能导致生殖细胞基因去抑制,进而导致脑细胞严重的身份危机——可能干扰正常的大脑发育。因此,生殖细胞基因的异位表达是定义这一 NDD 亚组的独特特征,并进一步表明生殖细胞基因沉默在大脑发育过程中的重要性。然而,生殖细胞基因表达对大脑发育的功能影响仍未确定。本文探讨了这种明显的体-生殖细胞转化是如何产生的,以及它如何通过基因组不稳定性和感觉纤毛形成受损来干扰神经发育。此外,我们还讨论了如何通过实验来检验这些假设,以最终确定异位生殖细胞转录本对与染色质相关的 NDD 的贡献。