Gene therapy and US healthcare: Rationalizing the price of promise.
作者信息
Koulianos Kollet
机构信息
National Hemophilia Foundation, New York, NY, USA.
出版信息
Mol Ther. 2021 Oct 6;29(10):2887-2888. doi: 10.1016/j.ymthe.2021.09.025. Epub 2021 Oct 1.
Abstract
摘要
相似文献
1
Gene therapy and US healthcare: Rationalizing the price of promise.基因疗法与美国医疗保健：为希望定价寻求合理性。
Mol Ther. 2021 Oct 6;29(10):2887-2888. doi: 10.1016/j.ymthe.2021.09.025. Epub 2021 Oct 1.
2
Landmark gene therapy poised for US approval.具有里程碑意义的基因疗法有望在美国获批。
Nat Rev Drug Discov. 2017 Oct 30;16(11):739-741. doi: 10.1038/nrd.2017.212.
3
The impact of regulatory policy on the development of somatic cell therapies in the United States.监管政策对美国体细胞疗法发展的影响。
Transpl Immunol. 2002 May;9(2-4):295-300. doi: 10.1016/s0966-3274(02)00012-6.
4
The Care Continuum: An Evolving Model for Care and Research in Rare Diseases.护理连续体：罕见病护理与研究的演进模式。
Pediatrics. 2017 Sep;140(3). doi: 10.1542/peds.2017-0108. Epub 2017 Aug 17.
5
BioMarin Defends Up-to-$3M List Price of Hemophilia A Gene Therapy.BioMarin为A型血友病基因疗法高达300万美元的标价进行辩护。
Hum Gene Ther. 2020 Aug;31(15-16):791-793. doi: 10.1089/hum.2020.29132.bfs.
6
What compassionate use means for gene therapies.基因疗法的同情用药意味着什么。
Nat Biotechnol. 2019 Apr;37(4):352-355. doi: 10.1038/s41587-019-0081-7.
7
National Institutes of Health, U.S. Food and Drug Administration, 15 Partners to Accelerate Development of Rare Disease Gene Therapies.美国国立卫生研究院、美国食品药品监督管理局，15个加速罕见病基因疗法开发的合作伙伴。
Hum Gene Ther. 2021 Dec;32(23-24):1420-1422. doi: 10.1089/hum.2021.29188.bfs.
8
Gene therapy for rare diseases: summary of a National Institutes of Health workshop, September 13, 2012.基因治疗罕见病：美国国立卫生研究院研讨会总结，2012 年 9 月 13 日。
Hum Gene Ther. 2013 Apr;24(4):355-62. doi: 10.1089/hum.2013.064.
9
Gene therapy and cancer: is it for everybody?基因疗法与癌症：它适用于所有人吗？
Cancer Invest. 1992;10(6):607-9. doi: 10.3109/07357909209024825.
10
Gene therapy: evidence, value and affordability in the US health care system.基因治疗：美国医疗体系中的证据、价值和可负担性。
J Comp Eff Res. 2018 Jan;7(1):15-28. doi: 10.2217/cer-2017-0068. Epub 2017 Nov 16.
引用本文的文献
1
Cost-Effectiveness of a Hypothetical Gene Therapy for Alzheimer's Disease: A Markov Simulation Analysis.一种假设的阿尔茨海默病基因疗法的成本效益：马尔可夫模拟分析
Innov Pharm. 2023 Nov 9;14(3). doi: 10.24926/iip.v14i3.5500. eCollection 2023.
Zotero 插件