Pediatrics, Women & Infants Hospital, Providence, RI, USA.
Center for Computational Molecular Biology, Brown Medical School, Brown University, Providence, RI, USA.
Sci Rep. 2022 Jan 10;12(1):438. doi: 10.1038/s41598-021-03427-0.
The likely genetic architecture of complex diseases is that subgroups of patients share variants in genes in specific networks sufficient to express a shared phenotype. We combined high throughput sequencing with advanced bioinformatic approaches to identify such subgroups of patients with variants in shared networks. We performed targeted sequencing of patients with 2 or 3 generations of preterm birth on genes, gene sets and haplotype blocks that were highly associated with preterm birth. We analyzed the data using a multi-sample, protein-protein interaction (PPI) tool to identify significant clusters of patients associated with preterm birth. We identified shared protein interaction networks among preterm cases in two statistically significant clusters, p < 0.001. We also found two small control-dominated clusters. We replicated these data on an independent, large birth cohort. Separation testing showed significant similarity scores between the clusters from the two independent cohorts of patients. Canonical pathway analysis of the unique genes defining these clusters demonstrated enrichment in inflammatory signaling pathways, the glucocorticoid receptor, the insulin receptor, EGF and B-cell signaling, These results support a genetic architecture defined by subgroups of patients that share variants in genes in specific networks and pathways which are sufficient to give rise to the disease phenotype.
复杂疾病的可能遗传结构是,亚组患者在特定网络中的基因变异足以表达共同的表型。我们结合高通量测序和先进的生物信息学方法,在共享网络中识别具有变异的此类患者亚组。我们对具有 2 或 3 代早产史的患者进行了靶向测序,对与早产高度相关的基因、基因集和单倍型块进行了靶向测序。我们使用多样本、蛋白质-蛋白质相互作用 (PPI) 工具分析数据,以识别与早产相关的显著患者集群。我们在两个具有统计学意义的聚类中鉴定了早产病例之间共享的蛋白质相互作用网络,p < 0.001。我们还发现了两个小的以对照为主的聚类。我们在一个独立的大型出生队列中复制了这些数据。分离测试显示,来自两个独立患者队列的聚类之间存在显著的相似性评分。这些聚类定义的独特基因的通路分析显示,炎症信号通路、糖皮质激素受体、胰岛素受体、EGF 和 B 细胞信号通路富集。这些结果支持了一种遗传结构,该结构由亚组患者定义,这些患者在特定网络和通路中的基因变异足以产生疾病表型。