Ou-Yang Fu, Li Chung-Liang, Chen Chia-Chi, Shen Yi-Chun, Moi Sin-Hua, Luo Chi-Wen, Xia Wei-Ya, Wang Ying-Nai, Lee Heng-Huan, Wang Lu-Hai, Wang Shao-Chun, Pan Mei-Ren, Hou Ming-Feng, Hung Mien-Chie
Division of Breast Oncology and Surgery, Department of Surgery, Kaohsiung Medical University Hospital Kaohsiung 80756, Taiwan.
Department of Pathology, E-Da Hospital and I-Shou University Kaohsiung 82445, Taiwan.
Am J Cancer Res. 2022 Jan 15;12(1):123-137. eCollection 2022.
The atezolizumab (Tecentriq), a humanized antibody against human programmed death ligand 1 (PD-L1), combined with nab-paclitaxel was granted with accelerated approval to treat unresectable locally advanced or metastatic triple-negative breast cancer (TNBC) due to the encouraging positive results of the phase 3 IMpassion130 trial using PD-L1 biomarker from immune cells to stratify patients. However, the post-market study IMpassion131 did not support the original observation, resulting in the voluntary withdrawal of atezolizumab from the indication in breast cancer by Genentech in 2021. Emerging evidence has revealed a high frequency of false negative result using the standard immunohistochemical (IHC) staining due to heavy glycosylation of PD-L1. The removal of glycosylation prevents from the false negative staining, enabling more accurate assessment of PD-L1 levels and improving prediction for response to immune checkpoint therapy. In the present study, the natural and de-glycosylated PD-L1 expression in tumor and immune cells from nine TNBC patients were analyzed by using clone 28-8 monoclonal antibody to correlate with treatment outcome. Our results demonstrate that: (1) Removal of the glycosylation indeed enhances the detection of PD-L1 by IHC staining, (2) The PD-L1 levels on tumor cell surface after removal of the glycosylation correlates well with clinical responses for atezolizumab treatment; (3) The criteria used in the IMpassion130 and IMpassion131 trials which scored the natural PD-L1 in the immune cells failed to correlate with the clinical response. Taken together, tumor cell surface staining of PD-L1 with de-glycosylation has a significant correlation with the clinical response for atezolizumab treatment, suggesting that treatment of atezolizumab may be worthy of further consideration with de-glycosylation procedure as a patient stratification strategy. A larger cohort to validate this important issue is warranted to ensure right patient population who could benefit from the existing FDA-approved drugs.
阿替利珠单抗(泰圣奇)是一种抗人程序性死亡配体1(PD-L1)的人源化抗体,与白蛋白结合型紫杉醇联合使用,因3期IMpassion130试验取得了令人鼓舞的阳性结果而被加速批准用于治疗不可切除的局部晚期或转移性三阴性乳腺癌(TNBC),该试验使用免疫细胞中的PD-L1生物标志物对患者进行分层。然而,上市后研究IMpassion131并不支持最初的观察结果,导致基因泰克公司于2021年自愿撤回阿替利珠单抗在乳腺癌适应症中的应用。新出现的证据表明,由于PD-L1的高度糖基化,使用标准免疫组织化学(IHC)染色会出现高频假阴性结果。去除糖基化可防止假阴性染色,能够更准确地评估PD-L1水平,并改善对免疫检查点治疗反应的预测。在本研究中,使用克隆28-8单克隆抗体分析了9例TNBC患者肿瘤和免疫细胞中天然和去糖基化的PD-L1表达,并将其与治疗结果相关联。我们的结果表明:(1)去除糖基化确实增强了IHC染色对PD-L1的检测;(2)去除糖基化后肿瘤细胞表面的PD-L1水平与阿替利珠单抗治疗的临床反应密切相关;(3)IMpassion130和IMpassion131试验中对免疫细胞中天然PD-L1进行评分的标准与临床反应无关。综上所述,去糖基化的PD-L1在肿瘤细胞表面的染色与阿替利珠单抗治疗的临床反应显著相关,这表明将去糖基化程序作为患者分层策略,阿替利珠单抗治疗可能值得进一步考虑。有必要进行更大规模的队列研究来验证这一重要问题,以确保正确的患者群体能够从现有的FDA批准药物中获益。