Division of Nephrology, Beth Israel Deaconess Medical Center, Harvard Medical School, Boston, Massachusetts, United States of America.
Division of Nephrology, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, United States of America.
PLoS One. 2022 Aug 1;17(8):e0272313. doi: 10.1371/journal.pone.0272313. eCollection 2022.
Mutations in TRPC6 are a cause of autosomal dominant focal segmental glomerulosclerosis in humans. Many of these mutations are known to have a gain-of-function effect on the non-specific cation channel function of TRPC6. In vitro studies have suggested these mutations affect several signaling pathways, but in vivo studies have largely compared wild-type and Trpc6-deficient rodents. We developed mice carrying a gain-of-function Trpc6 mutation encoding an E896K amino acid change, corresponding to a known FSGS mutation in TRPC6. Homozygous mutant Trpc6 animals have no appreciable renal pathology, and do not develop albuminuria until very advanced age. The Trpc6E896K mutation does not impart susceptibility to PAN nephrosis. The animals show a slight delay in recovery from the albumin overload model. In response to chronic angiotensin II infusion, Trpc6E896K/E896K mice have slightly greater albuminuria initially compared to wild-type animals, an effect that is lost at later time points, and a statistically non-significant trend toward more glomerular injury. This phenotype is nearly opposite to that of Trpc6-deficient animals previously described. The Trpc6 mutation does not appreciably impact renal interstitial fibrosis in response to either angiotensin II infusion, or folate-induced kidney injury. TRPC6 protein and TRPC6-agonist induced calcium influx could not be detected in glomeruli. In sum, these findings suggest that a gain-of-function Trpc6 mutation confers only a mild susceptibility to glomerular injury in the mouse.
TRPC6 基因突变是人类常染色体显性局灶节段性肾小球硬化症的一个病因。许多这些突变已知对 TRPC6 的非特异性阳离子通道功能具有获得性功能效应。体外研究表明这些突变影响几种信号通路,但体内研究主要比较野生型和 Trpc6 缺陷型啮齿动物。我们开发了携带编码 E896K 氨基酸变化的获得性功能 Trpc6 突变的小鼠,该突变对应于 TRPC6 中的已知 FSGS 突变。纯合突变 Trpc6 动物没有明显的肾脏病理学,并且直到非常老年时才发展为白蛋白尿。Trpc6E896K 突变不会赋予对 PAN 肾病的易感性。这些动物在从白蛋白过载模型中恢复时略有延迟。对慢性血管紧张素 II 输注的反应,Trpc6E896K/E896K 小鼠与野生型动物相比最初具有稍高的白蛋白尿,该效应在以后的时间点丢失,并且肾小球损伤的统计学意义上无显著性趋势。这种表型与以前描述的 Trpc6 缺陷型动物的表型几乎相反。TRPC6 突变对血管紧张素 II 输注或叶酸诱导的肾脏损伤均不会显著影响肾间质纤维化。在肾小球中不能检测到 TRPC6 蛋白和 TRPC6 激动剂诱导的钙内流。总之,这些发现表明获得性功能 Trpc6 突变仅赋予小鼠肾小球损伤的轻度易感性。