Current and Future Therapeutical Aspects of X-Linked Hypophosphatemia in Children With Special Attention to Klotho/Fibroblast Growth Factor 23 System.
作者信息
Bittmann Stefan, Moschuring-Alieva Elena, Luchter Elisabeth, Villalon Gloria
机构信息
Department of Pediatrics, Ped Mind Institute, Hindenburgring 4, D-48599 Gronau, Germany.
出版信息
J Clin Med Res. 2022 Oct;14(10):436-439. doi: 10.14740/jocmr4820. Epub 2022 Oct 28.
Abstract
摘要
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Sci Adv. 2021 Oct 29;7(44):eabj5018. doi: 10.1126/sciadv.abj5018. Epub 2021 Oct 27.
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Sustained Efficacy and Safety of Burosumab, a Monoclonal Antibody to FGF23, in Children With X-Linked Hypophosphatemia.Burosumab，一种成纤维细胞生长因子 23 的单克隆抗体，在 X 连锁低磷血症儿童中的持续疗效和安全性。
J Clin Endocrinol Metab. 2022 Feb 17;107(3):813-824. doi: 10.1210/clinem/dgab729.
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X-Linked Hypophosphatemic Rickets: Multisystemic Disorder in Children Requiring Multidisciplinary Management.X 连锁低磷血症性佝偻病：需要多学科管理的儿童多系统疾病。
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