轻度和中度甲型血友病：被忽视的病症，需求仍未得到满足。
Mild and Moderate Hemophilia A: Neglected Conditions, Still with Unmet Needs.
作者信息
Castaman Giancarlo, Peyvandi Flora, De Cristofaro Raimondo, Pollio Berardino, Di Minno Dario M N
机构信息
Centre for Bleeding Disorders and Coagulation, Careggi University Hospital, 50134 Florence, Italy.
Complex Operative Unit of General Medicine-Hemostasis and Thrombosis, IRCCS Ca' Granda Foundation Ospedale Maggiore Policlinico, 20122 Milan, Italy.
出版信息
J Clin Med. 2023 Feb 8;12(4):1368. doi: 10.3390/jcm12041368.
Abstract
Hemophilia A (HA) is an inherited X-linked bleeding disorder, caused by the deficiency of coagulation factor VIII (FVIII), with variable clinical phenotypes [...].
摘要
甲型血友病（HA）是一种遗传性X连锁出血性疾病，由凝血因子VIII（FVIII）缺乏引起，具有多种临床表型[...]。
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