Antonini Giovanni, Habetswallner Francesco, Inghilleri Maurizio, Mantegazza Renato, Rodolico Carmelo, Saccà Francesco, Sgarzi Manlio, deRuyck Femke, Paci Sandra, Phillips Glenn, Crippa Laura, Veronesi Chiara, Perrone Valentina, Degli Esposti Luca
Department of Neurology Mental Health and Sensory Organs (NESMOS), Faculty of Medicine and Psychology, University of Rome La Sapienza, Rome, Italy.
Clinical Neurophysiology Unit, Cardarelli Hospital, Naples, Italy.
Heliyon. 2023 May 20;9(6):e16367. doi: 10.1016/j.heliyon.2023.e16367. eCollection 2023 Jun.
The purpose of this study was to investigate the epidemiology, management, and economic burden of myasthenia gravis in settings of real clinical practice. The analysis used administrative databases covering around 12 million subjects across Italy and included all adult patients with hospitalization discharge diagnosis or active exemption code for myasthenia gravis or with ≥1 pyridostigmine prescription from 2011 to 2018. The estimated prevalence of myasthenia gravis during 2018 was in the range 13.5-29.3/100,000 people (depending on the criteria applied), corresponding to 8190-17,728 alive patients, when reproportioning data to the entire Italian population. Overall 4397 patients with myasthenia gravis (mean age 61.7 years, 46.6% males) were included. A large pyridostigmine use was observed (84.0%-46.8% from 1st to 3rd year of follow-up), followed by corticosteroids (54.5%-44.6% from 1st to 3rd year of follow-up) and non-steroidal immunosuppressants (16% over follow-up). Total direct healthcare costs for myasthenia gravis were 4-times higher than those of the general population (€3771 and €869, respectively), and up to 9-fold increased when considering patients with exacerbation (€7827). These findings showed the epidemiologic burden of myasthenia gravis and the complexity of the therapeutic management for the affected patients, with large use of treatments and elevated healthcare expenditures.
本研究的目的是调查重症肌无力在实际临床实践中的流行病学、管理情况及经济负担。该分析使用了涵盖意大利约1200万受试者的行政数据库,纳入了2011年至2018年期间所有因重症肌无力住院出院诊断或有活动豁免代码或开具≥1次溴吡斯的明处方的成年患者。2018年重症肌无力的估计患病率在13.5 - 29.3/10万之间(取决于所应用的标准),将数据重新按比例推算至整个意大利人口时,相当于8190 - 17728名存活患者。总共纳入了4397例重症肌无力患者(平均年龄61.7岁,男性占46.6%)。观察到大量使用溴吡斯的明(随访第1年至第3年为84.0% - 46.8%),其次是皮质类固醇(随访第1年至第3年为54.5% - 44.6%)和非甾体类免疫抑制剂(随访期间为16%)。重症肌无力的直接医疗总费用比普通人群高4倍(分别为3771欧元和869欧元),考虑病情加重的患者时费用增加高达9倍(7827欧元)。这些发现显示了重症肌无力的流行病学负担以及受影响患者治疗管理的复杂性,治疗使用量大且医疗支出高昂。