Aoi Yoko, Kato Yuta, Asano Kunihito, Otsubo Yasuto, Uyama Yoshiaki
Office of New Drug V, Pharmaceuticals and Medical Devices Agency (PMDA), Tokyo, 100-0013, Japan.
Office of New Drug III, Pharmaceuticals and Medical Devices Agency (PMDA), Tokyo, 100-0013, Japan.
Ther Innov Regul Sci. 2023 Nov;57(6):1298-1303. doi: 10.1007/s43441-023-00566-6. Epub 2023 Aug 16.
Although the percentage of multi-regional clinical trials (MRCTs) submitted for drug approval in Japan increased significantly since the 2007 publication of the regulatory guideline, "Basic principles on global clinical trials", strategic collaborations between Asian countries will be important to promote MRCTs in accordance with the ICH E17 guideline published in 2017. In this study, characteristics of MRCTs reviewed for drug approval in Japan, especially those with participation by South-East Asia and East Asia, were investigated to explore opportunities for collaborations on global drug development in Asia. More than 90% of reviewed trials were conducted as global MRCTs. In addition to Japan, South-East Asia has participated in various types of MRCTs in terms of total numbers of subjects and countries. However, South-East Asia participation was lower in large-size MRCTs (total sample size ≥ 1000) than in middle- (500 ≤ total sample size < 1000) and small-size MRCTs (total sample size < 500). Furthermore, similar clinical trials for the same indications to the MRCTs without South-East Asia were rarely conducted separately in South-East Asia. Participation of other Asian countries did not affect the percentage of Japanese subjects enrolled in an MRCT, but did significantly increase the percentage of participating Asian subjects. These results suggest that additional opportunities for collaboration on MRCTs may be possible between Japan and other Asian countries, especially more collaborations with South-East Asia in the large-size MRCTs. More data of Asian populations from MRCTs will be useful for exploring an important ethnic factor affecting drug response, and will provide a sound scientific basis in considering the application of the pooled data concept in Asia, as described in the ICH E17 guideline.
尽管自2007年发布监管指南《全球临床试验基本原则》以来,在日本提交药物审批的多区域临床试验(MRCT)的比例显著增加,但根据2017年发布的ICH E17指南,亚洲国家之间的战略合作对于推动MRCT至关重要。在本研究中,对在日本进行药物审批审查的MRCT的特征进行了调查,尤其是那些有东南亚和东亚参与的试验,以探索亚洲全球药物开发的合作机会。超过90%的审查试验作为全球MRCT进行。除日本外,东南亚在受试者总数和参与国家方面参与了各种类型的MRCT。然而,东南亚在大型MRCT(总样本量≥1000)中的参与度低于中型(500≤总样本量<1000)和小型MRCT(总样本量<500)。此外,在东南亚很少单独进行与没有东南亚参与的MRCT具有相同适应症的类似临床试验。其他亚洲国家的参与并未影响MRCT中日本受试者的比例,但显著增加了参与的亚洲受试者的比例。这些结果表明,日本与其他亚洲国家之间在MRCT方面可能有更多合作机会,特别是在大型MRCT中与东南亚有更多合作。来自MRCT的更多亚洲人群数据将有助于探索影响药物反应的重要种族因素,并将为考虑如ICH E17指南所述在亚洲应用汇总数据概念提供坚实的科学依据。