Editorial: Gene therapy for the central and peripheral nervous system, volume II.
作者信息
Tosolini Andrew P, Smith George M
机构信息
Department of Neuromuscular Diseases, Queen Square Institute of Neurology, University College London, London, United Kingdom.
UCL Queen Square Motor Neuron Disease Centre, University College London, London, United Kingdom.
出版信息
Front Mol Neurosci. 2023 Aug 1;16:1258458. doi: 10.3389/fnmol.2023.1258458. eCollection 2023.
Abstract
摘要
相似文献
1
Editorial: Gene therapy for the central and peripheral nervous system, volume II.社论：中枢和周围神经系统的基因治疗，第二卷。
Front Mol Neurosci. 2023 Aug 1;16:1258458. doi: 10.3389/fnmol.2023.1258458. eCollection 2023.
2
Editorial: Gene Therapy for the Central and Peripheral Nervous System.
Front Mol Neurosci. 2018 Feb 22;11:54. doi: 10.3389/fnmol.2018.00054. eCollection 2018.
3
Immune-mediated diseases involving central and peripheral nervous systems.涉及中枢和外周神经系统的免疫介导性疾病。
Eur J Neurol. 2023 Feb;30(2):490-500. doi: 10.1111/ene.15628. Epub 2022 Nov 27.
4
AAV Targeting of Glial Cell Types in the Central and Peripheral Nervous System and Relevance to Human Gene Therapy.腺相关病毒对中枢和外周神经系统中神经胶质细胞类型的靶向作用及其与人类基因治疗的相关性
Front Mol Neurosci. 2021 Jan 11;13:618020. doi: 10.3389/fnmol.2020.618020. eCollection 2020.
5
CNS Transduction Benefits of AAV-PHP.eB over AAV9 Are Dependent on Administration Route and Mouse Strain.与AAV9相比，AAV-PHP.eB在中枢神经系统转导方面的优势取决于给药途径和小鼠品系。
Mol Ther Methods Clin Dev. 2020 Oct 20;19:447-458. doi: 10.1016/j.omtm.2020.10.011. eCollection 2020 Dec 11.
6
Netrin 1 and Dcc signalling are required for confinement of central axons within the central nervous system.Netrin 1 和 Dcc 信号对于中枢轴突在中枢神经系统内的限制是必需的。
Development. 2014 Feb;141(3):594-603. doi: 10.1242/dev.099606.
7
Challenges in adeno-associated virus-based treatment of central nervous system diseases through systemic injection.通过系统注射用腺相关病毒治疗中枢神经系统疾病的挑战。
Life Sci. 2021 Apr 1;270:119142. doi: 10.1016/j.lfs.2021.119142. Epub 2021 Jan 30.
8
Gene therapy and peripheral nerve repair: a perspective.基因治疗与周围神经修复：一种观点。
Front Mol Neurosci. 2015 Jul 15;8:32. doi: 10.3389/fnmol.2015.00032. eCollection 2015.
9
A Subpopulation of Foxj1-Expressing, Nonmyelinating Schwann Cells of the Peripheral Nervous System Contribute to Schwann Cell Remyelination in the Central Nervous System.外周神经系统中 Foxj1 表达的非髓鞘形成 Schwann 细胞亚群有助于中枢神经系统的 Schwann 细胞髓鞘再生。
J Neurosci. 2018 Oct 24;38(43):9228-9239. doi: 10.1523/JNEUROSCI.0585-18.2018. Epub 2018 Sep 18.
10
VEGF - A Stimulus for Neuronal Development and Regeneration in the CNS and PNS.血管内皮生长因子A：中枢神经系统和周围神经系统中神经元发育与再生的刺激因素
Curr Protein Pept Sci. 2018;19(6):589-597. doi: 10.2174/1389203719666180104113937.
本文引用的文献
1
BBB opening with focused ultrasound in nonhuman primates and Parkinson's disease patients: Targeted AAV vector delivery and PET imaging.在非人灵长类动物和帕金森病患者中使用聚焦超声打开 BBB：靶向 AAV 载体传递和 PET 成像。
Sci Adv. 2023 Apr 21;9(16):eadf4888. doi: 10.1126/sciadv.adf4888. Epub 2023 Apr 19.
2
Boosting peripheral BDNF rescues impaired in vivo axonal transport in CMT2D mice.增强外周 BDNF 可挽救 CMT2D 小鼠体内受损的轴突运输。
JCI Insight. 2023 May 8;8(9):e157191. doi: 10.1172/jci.insight.157191.
3
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders.用半理性生物工程方法改造 AAV 载体，以提高其效力和特异性，用于肌肉疾病的系统性基因治疗。
Sci Adv. 2022 Sep 23;8(38):eabn4704. doi: 10.1126/sciadv.abn4704. Epub 2022 Sep 21.
4
Adeno-Associated Virus Toolkit to Target Diverse Brain Cells.腺相关病毒工具包可用于靶向多种脑内细胞。
Annu Rev Neurosci. 2022 Jul 8;45:447-469. doi: 10.1146/annurev-neuro-111020-100834. Epub 2022 Apr 19.
5
Viral vector-based gene therapies in the clinic.临床中基于病毒载体的基因疗法。
Bioeng Transl Med. 2021 Oct 20;7(1):e10258. doi: 10.1002/btm2.10258. eCollection 2022 Jan.
6
AAV capsid variants with brain-wide transgene expression and decreased liver targeting after intravenous delivery in mouse and marmoset.在小鼠和狨猴静脉注射后具有全脑转基因表达且肝脏靶向性降低的腺相关病毒衣壳变体。
Nat Neurosci. 2022 Jan;25(1):106-115. doi: 10.1038/s41593-021-00969-4. Epub 2021 Dec 9.
7
Intramuscular Delivery of Gene Therapy for Targeting the Nervous System.用于靶向神经系统的基因治疗的肌肉注射给药
Front Mol Neurosci. 2020 Jul 17;13:129. doi: 10.3389/fnmol.2020.00129. eCollection 2020.
8
Optimization of adeno-associated viral vector-mediated transduction of the corticospinal tract: comparison of four promoters.优化腺相关病毒载体介导的皮质脊髓束转导：四种启动子的比较。
Gene Ther. 2021 Feb;28(1-2):56-74. doi: 10.1038/s41434-020-0169-1. Epub 2020 Jun 23.
9
Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS.鞘内脊髓递送达 AAV9 可实现广泛的基因沉默并阻止 ALS 运动神经元变性。
Nat Med. 2020 Jan;26(1):118-130. doi: 10.1038/s41591-019-0674-1. Epub 2019 Dec 23.
10
Editorial: Gene Therapy for the Central and Peripheral Nervous System.
Front Mol Neurosci. 2018 Feb 22;11:54. doi: 10.3389/fnmol.2018.00054. eCollection 2018.
Zotero 插件