Department of Molecular Genetics and the National Tumour Biology Laboratory, National Institute of Oncology, Comprehensive Cancer Center, Budapest, Hungary.
Department of Oncology Biobank, National Institute of Oncology, Comprehensive Cancer Center, Budapest, Hungary.
Sci Rep. 2023 Aug 31;13(1):14259. doi: 10.1038/s41598-023-41481-y.
TP53 variant interpretation is still challenging, especially in patients with attenuated Li-Fraumeni syndrome (LFS). We investigated the prevalence of pathogenic/likely pathogenic (P/LP) variants and LFS disease in the Hungarian population of cancer patients. By testing 893 patients with multiplex or familial cancer, we identified and functionally characterized novel splice variants of TP53 helping accurate variant classification. The differences among various semi-automated interpretation platforms without manual curation highlight the importance of focused interpretation as the automatic classification systems do not apply the TP53-specific criteria. The predicted frequency of the TP53 P/LP variants in Hungary is 0.3 per million which most likely underestimates the real prevalence. The higher detection rate of disease-causing variants in patients with attenuated LFS phenotype compared to the control population (OR 12.5; p < 0.0001) may raise the potential benefit of the TP53 genetic testing as part of the hereditary cancer panels of patients with multiple or familial cancer even when they do not meet Chompret criteria. Tumours developed at an earlier age in phenotypic LFS patients compared to the attenuated LFS patients which complicates genetic counselling as currently there are no different recommendations in surveillance protocols for LFS, phenotypic LFS, and attenuated LFS patients.
TP53 变异的解读仍然具有挑战性,特别是在轻衰弱型 Li-Fraumeni 综合征(LFS)患者中。我们研究了致病性/可能致病性(P/LP)变异体和匈牙利癌症患者中 LFS 疾病的流行情况。通过对 893 名多发性或家族性癌症患者进行检测,我们鉴定并功能表征了新的 TP53 剪接变异体,有助于准确的变异分类。在没有人工策管的各种半自动解释平台之间存在差异,突出了重点解释的重要性,因为自动分类系统并未应用 TP53 特定的标准。匈牙利的 TP53 P/LP 变异体的预测频率为每百万 0.3,这很可能低估了实际的流行率。与对照人群相比,轻衰弱型 LFS 表型患者中导致疾病的变异体的检测率更高(OR 12.5;p<0.0001),这可能会提高 TP53 基因检测作为多发性或家族性癌症患者遗传性癌症检测的一部分的潜在益处,即使他们不符合 Chompret 标准。表型 LFS 患者的肿瘤发病年龄比轻衰弱型 LFS 患者更早,这使得遗传咨询变得复杂,因为目前在 LFS、表型 LFS 和轻衰弱型 LFS 患者的监测方案中没有不同的建议。