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A phase 2 prospective study of bortezomib, cyclophosphamide, and dexamethasone in patients with newly diagnosed iMCD.一项针对新诊断的免疫性血小板减少性紫癜患者使用硼替佐米、环磷酰胺和地塞米松的2期前瞻性研究。 (注:原文中iMCD可能有误,推测为ITP即免疫性血小板减少性紫癜,若不是该病症请根据准确信息修改译文)
Blood. 2023 May 25;141(21):2654-2657. doi: 10.1182/blood.2023020009.
2
Treatment-resistant idiopathic multicentric Castleman disease with thrombocytopenia, anasarca, fever, reticulin fibrosis, renal dysfunction, and organomegaly managed with Janus kinase inhibitors: A case report.伴有血小板减少、全身水肿、发热、网状纤维纤维化、肾功能不全和器官肿大的难治性特发性多中心 Castleman 病采用 Janus 激酶抑制剂治疗:一例报告。
Medicine (Baltimore). 2022 Dec 2;101(48):e32200. doi: 10.1097/MD.0000000000032200.
3
Discovery and validation of a novel subgroup and therapeutic target in idiopathic multicentric Castleman disease.特发性多中心Castleman病中一个新亚组及治疗靶点的发现与验证
Blood Adv. 2021 Sep 14;5(17):3445-3456. doi: 10.1182/bloodadvances.2020004016.
4
JAK1/2 Inhibition in Severe TAFRO Syndrome: A Case Report.JAK1/2 抑制剂治疗重症TAFRO综合征:一例报告
Ann Intern Med. 2021 May;174(5):719-721. doi: 10.7326/L20-1051. Epub 2021 Jan 12.
5
Increased mTOR activation in idiopathic multicentric Castleman disease.特发性多中心 Castleman 病中 mTOR 激活增加。
Blood. 2020 May 7;135(19):1673-1684. doi: 10.1182/blood.2019002792.
6
Phase 2 study using oral thalidomide-cyclophosphamide-prednisone for idiopathic multicentric Castleman disease.采用口服沙利度胺-环磷酰胺-泼尼松治疗特发性多中心 Castleman 病的 2 期研究。
Blood. 2019 Apr 18;133(16):1720-1728. doi: 10.1182/blood-2018-11-884577. Epub 2019 Feb 13.
7
International, evidence-based consensus treatment guidelines for idiopathic multicentric Castleman disease.特发性多中心 Castleman 病的国际、循证共识治疗指南。
Blood. 2018 Nov 15;132(20):2115-2124. doi: 10.1182/blood-2018-07-862334. Epub 2018 Sep 4.
8
International, evidence-based consensus diagnostic criteria for HHV-8-negative/idiopathic multicentric Castleman disease.HHV-8阴性/特发性多中心Castleman病的国际循证共识诊断标准。
Blood. 2017 Mar 23;129(12):1646-1657. doi: 10.1182/blood-2016-10-746933. Epub 2017 Jan 13.
9
Siltuximab for multicentric Castleman's disease: a randomised, double-blind, placebo-controlled trial.西妥昔单抗治疗多发性 Castleman 病的随机、双盲、安慰剂对照试验。
Lancet Oncol. 2014 Aug;15(9):966-74. doi: 10.1016/S1470-2045(14)70319-5. Epub 2014 Jul 17.
10
A double-blind, placebo-controlled trial of ruxolitinib for myelofibrosis.芦可替尼治疗骨髓纤维化的双盲、安慰剂对照试验。
N Engl J Med. 2012 Mar 1;366(9):799-807. doi: 10.1056/NEJMoa1110557.

Ruxolitinib for the Treatment of Refractory Idiopathic Multicentric Castleman Disease: A Case Report.

作者信息

Gao Yu-Han, Duan Ming-Hui, Li Jian, Zhang Lu

机构信息

Peking Union Medical College Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Department of Hematology, Beijing, China

出版信息

Turk J Haematol. 2024 Mar 1;41(1):61-63. doi: 10.4274/tjh.galenos.2024.2023.0477. Epub 2024 Feb 15.

DOI:10.4274/tjh.galenos.2024.2023.0477
PMID:38356196
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC10918405/
Abstract
摘要