Department of Industrial Engineering and Operations Research (IEOR), Columbia University, New York City, NY.
Gu and Elsisi served as co-first authors and contributed equally to the work.
J Manag Care Spec Pharm. 2024 Apr;30(4):376-385. doi: 10.18553/jmcp.2024.30.4.376.
Little is known regarding the geographic disparity in the distribution of phase 1-3 clinical trials of new cancer treatments in the US and the associated factors.
To examine county-level variation in the number of phase 1-3 cancer clinical trials and the associations between county characteristics and having phase 1-3 cancer clinical trials.
We identified phase 1-3 cancer clinical trials started in the US between January 2008 and December 2022 from the Aggregate Analysis of ClinicalTrials.gov database. We analyzed the distribution of phase 1-3 cancer clinical trials at the county level. Using a mixed-effects regression with states as random intercepts, we estimated the associations between a county's median age, median household income, percentage of population from racial and ethnic minority groups, proportion of population aged 25 years or older with an educational attainment of bachelor's degree or higher, rurality, cancer incidence rate, and number of medical oncologists per population with having any phase 1-3 cancer clinical trial in a county.
After excluding trials that were suspended, terminated, and withdrawn, a total of 14,977 phase 1-3 cancer clinical trials started in the United States between January 2008 and December 2022 were included in the primary analysis. Only 1,333 out of 3,143 counties (42.4%) had 1 or more trial during this period. Counties that were rural, with lower median household income, a less educated population, fewer medical oncologists per population, and lower cancer incidence rates demonstrated a significantly lower likelihood of having phase 1-3 cancer clinical trials.
Our study revealed substantial geographic disparities in the distribution of phase 1-3 cancer clinical trials. Limited trial availability in low-income, low-education, low-oncologist, and rural areas can be a significant barrier to patient participation, potentially hindering adoption and worsening outcomes in disadvantaged populations.
在美国,关于新癌症治疗方法的 1 期至 3 期临床试验在各地区的分布情况及其相关因素,人们知之甚少。
本研究旨在探讨美国县一级 1 期至 3 期癌症临床试验数量的差异,并分析县特征与开展 1 期至 3 期癌症临床试验之间的关联。
我们从 Aggregate Analysis of ClinicalTrials.gov 数据库中确定了 2008 年 1 月至 2022 年 12 月期间在美国开展的 1 期至 3 期癌症临床试验。我们分析了县一级的 1 期至 3 期癌症临床试验分布情况。采用包含州作为随机截距的混合效应回归模型,估计了县的中位年龄、家庭中位收入、少数族裔人口比例、25 岁及以上人群中具有学士学位或更高学历的比例、农村程度、癌症发病率以及每人口中肿瘤内科医生数量与该县开展任何 1 期至 3 期癌症临床试验之间的关联。
在排除暂停、终止和撤回的试验后,共有 14977 项 1 期至 3 期癌症临床试验于 2008 年 1 月至 2022 年 12 月期间在美国开始纳入主要分析。在此期间,只有 3143 个县中的 1333 个(42.4%)有 1 项或多项试验。农村地区、家庭中位收入较低、人口教育程度较低、每人口中肿瘤内科医生数量较少、癌症发病率较低的县开展 1 期至 3 期癌症临床试验的可能性显著降低。
本研究揭示了 1 期至 3 期癌症临床试验在分布上存在显著的地域差异。低收入、低教育、低肿瘤内科医生数量和农村地区的试验机会有限,可能成为患者参与的重大障碍,从而潜在地阻碍了弱势人群的治疗方法的采用和改善结局。