Department of Medicine A, Haematology and Oncology, University Hospital Muenster, Muenster, Germany.
Institute of Medical Informatics, University of Muenster, Muenster, Germany.
Br J Haematol. 2024 Jul;205(1):280-290. doi: 10.1111/bjh.19552. Epub 2024 Jun 4.
For patients with relapsed or refractory AML, sequential conditioning prior to allogeneic stem cell transplantation (alloSCT) is an established and potentially curative treatment option. Early response to treatment during conditioning indicates chemotherapy-responsive disease and may have prognostic value. We retrospectively evaluated blast clearance on day 5 after melphalan, administered 11 days prior to alloSCT as part of a sequential conditioning in 176 patients with active AML. Overall survival (OS) was 52% (95% confidence interval [CI] 45%-60%), and relapse-free survival (RFS) was 47% (95% CI 40%-55%) at 3 years. Patients who achieved early blast clearance did not show a significant improvement in OS and RFS (OS, hazard ratio [HR] HR 0.75, p 0.19; RFS, HR 0.71, p 0.09, respectively), but had a significantly lower non-relapse mortality rate (HR 0.46, p 0.017). HLA-mismatched donor, older age, adverse genetic risk and higher comorbidity scores were associated with inferior survival outcomes. A high initial blast count was only associated with inferior prognosis in patients receiving chemotherapy-only compared to total body irradiation containing conditioning therapy. These results indicate that for patients transplanted with active AML, sensitivity to chemotherapy might be of less importance, compared to other disease- and transplant-related factors.
对于复发或难治性急性髓系白血病(AML)患者,在异基因造血干细胞移植(alloSCT)前进行序贯预处理是一种既定的、潜在可治愈的治疗选择。预处理期间的早期治疗反应表明疾病对化疗敏感,可能具有预后价值。我们回顾性评估了 176 例活动性 AML 患者接受 alloSCT 前 11 天接受马法兰预处理后第 5 天的原始细胞清除情况。3 年时的总生存率(OS)为 52%(95%置信区间 [CI] 45%-60%),无复发生存率(RFS)为 47%(95% CI 40%-55%)。早期原始细胞清除的患者在 OS 和 RFS 方面并未显著改善(OS:风险比 [HR] 0.75,p 0.19;RFS:HR 0.71,p 0.09),但非复发死亡率显著降低(HR 0.46,p 0.017)。HLA 错配供体、年龄较大、不良遗传学风险和较高的合并症评分与较差的生存结果相关。与仅接受化疗的患者相比,在接受包含全身照射的预处理治疗的患者中,高初始原始细胞计数仅与化疗敏感性较差相关。这些结果表明,与其他疾病和移植相关因素相比,对于接受移植治疗的活动性 AML 患者,对化疗的敏感性可能没有那么重要。