Søndergaard Henning
Danish Kidney Association, Taastrup, Denmark.
Patient Prefer Adherence. 2024 May 31;18:1059-1064. doi: 10.2147/PPA.S445399. eCollection 2024.
The inclusion of patient representatives as study consultants brings diverse perspectives, insights, and experiences to clinical trial design and execution, and their role in the clinical trial development process is being increasingly recognized and valued. The APPETIZE study evaluated the palatability of, and preference for, three potassium binders for treating hyperkalemia in patients with chronic kidney disease. A core aspect of the development of this study was the inclusion of a patient representative during the design stage. Here, I describe the process of patient involvement in the APPETIZE study design (ClinicalTrials.gov Identifier: NCT04566653), the resultant positive impacts, and key learnings. A patient with chronic kidney disease was invited to be a member of the APPETIZE trial design team. This patient representative attended study team meetings and provided invaluable input into protocol development, questionnaire selection, design of patient information sheets and consent forms, and primary manuscript structure. These critical insights resulted in an enhanced trial design and generation of high-quality, patient-relevant data. APPETIZE provides an excellent example of a patient preference study that relied on input from multiple stakeholder groups, including, most notably, the patients themselves. This approach may serve as a model for early and deep patient engagement in the design and interpretation of clinical trials.
将患者代表纳入研究顾问团队,能为临床试验的设计和实施带来多样的观点、见解和经验,他们在临床试验开发过程中的作用也日益得到认可和重视。APPETIZE研究评估了三种用于治疗慢性肾病患者高钾血症的钾结合剂的适口性和患者偏好。该研究开展过程的一个核心方面是在设计阶段纳入了一名患者代表。在此,我描述患者参与APPETIZE研究设计的过程(ClinicalTrials.gov标识符:NCT04566653)、由此产生的积极影响以及关键经验教训。一名慢性肾病患者受邀成为APPETIZE试验设计团队的成员。这位患者代表参加了研究团队会议,并在方案制定、问卷选择、患者信息表和知情同意书设计以及主要稿件结构方面提供了宝贵意见。这些关键见解促成了试验设计的改进以及高质量、与患者相关数据的产生。APPETIZE为一项患者偏好研究提供了一个绝佳范例,该研究依赖于多个利益相关者群体的意见,其中最显著的是患者自身。这种方法可作为患者在临床试验设计和解读中早期深度参与的典范。