Department of Pediatrics, Children's Hospital of New Orleans, New Orleans, Louisiana, USA.
Department of Pediatrics, Tulane University, New Orleans, Louisiana, USA.
Pediatr Pulmonol. 2024 Dec;59(12):3106-3116. doi: 10.1002/ppul.27190. Epub 2024 Jul 26.
This past year, there were many important advances for patients with cystic fibrosis (CF). Of the many publications related to CF in 2023, there was further evaluation of highly effective modulator therapy, new assessments and guidelines for clinical manifestations and therapies for CF, advances in newborn screening and diagnosis, and evaluation of outcomes for people with CF transmembrane conductance regulator-related metabolic syndrome/CF screen positive, inconclusive diagnosis. The aim of this review article is not to provide a full assessment of the wide range of articles published in 2023, but to provide a brief review of publication that may lead to changes in clinical care.
过去一年，囊性纤维化（CF）患者取得了许多重要进展。在 2023 年与 CF 相关的众多出版物中，进一步评估了高效调节剂治疗、CF 临床表现和治疗的新评估和指南、新生儿筛查和诊断的进展，以及 CF 跨膜电导调节因子相关代谢综合征/CF 筛查阳性、结果不确定诊断人群的结局评估。本文的目的不是对 2023 年发表的大量文章进行全面评估，而是简要回顾可能导致临床护理变化的出版物。
