Department of Biochemistry and Pharmacogenomics, Faculty of Pharmacy, Medical University of Warsaw, 02-097 Warsaw, Poland.
Centre for Preclinical Research, Medical University of Warsaw, 02-097 Warsaw, Poland.
Int J Mol Sci. 2024 Jul 15;25(14):7743. doi: 10.3390/ijms25147743.
Chimeric antigen receptor T-cell (CAR-T) therapy is a novel anticancer therapy using autologous or allogeneic T-cells. To date, six CAR-T therapies for specific B-cell acute lymphoblastic leukemia (B-ALL), non-Hodgkin lymphomas (NHL), and multiple myeloma (MM) have been approved by the Food and Drug Administration (FDA). Significant barriers to the effectiveness of CAR-T therapy include cytokine release syndrome (CRS), neurotoxicity in the case of Allogeneic Stem Cell Transplantation (Allo-SCT) graft-versus-host-disease (GVHD), antigen escape, modest antitumor activity, restricted trafficking, limited persistence, the immunosuppressive microenvironment, and senescence and exhaustion of CAR-Ts. Furthermore, cancer drug resistance remains a major problem in clinical practice. CAR-T therapy, in combination with checkpoint blockades and bispecific T-cell engagers (BiTEs) or other drugs, appears to be an appealing anticancer strategy. Many of these agents have shown impressive results, combining efficacy with tolerability. Biomarkers like extracellular vesicles (EVs), cell-free DNA (cfDNA), circulating tumor (ctDNA) and miRNAs may play an important role in toxicity, relapse assessment, and efficacy prediction, and can be implicated in clinical applications of CAR-T therapy and in establishing safe and efficacious personalized medicine. However, further research is required to fully comprehend the particular side effects of immunomodulation, to ascertain the best order and combination of this medication with conventional chemotherapy and targeted therapies, and to find reliable predictive biomarkers.
嵌合抗原受体 T 细胞(CAR-T)疗法是一种利用自体或异体 T 细胞的新型抗癌疗法。迄今为止,六种用于特定 B 细胞急性淋巴细胞白血病(B-ALL)、非霍奇金淋巴瘤(NHL)和多发性骨髓瘤(MM)的 CAR-T 疗法已获得美国食品和药物管理局(FDA)的批准。CAR-T 疗法有效性的显著障碍包括细胞因子释放综合征(CRS)、同种异体干细胞移植(Allo-SCT)移植物抗宿主病(GVHD)的神经毒性、抗原逃逸、抗肿瘤活性适中、受限的迁移、有限的持久性、免疫抑制微环境以及 CAR-T 的衰老和衰竭。此外,癌症耐药性仍然是临床实践中的一个主要问题。CAR-T 疗法与检查点阻断和双特异性 T 细胞衔接器(BiTEs)或其他药物联合使用,似乎是一种有吸引力的抗癌策略。其中许多药物已显示出令人印象深刻的结果,将疗效与耐受性相结合。生物标志物如细胞外囊泡(EVs)、无细胞 DNA(cfDNA)、循环肿瘤(ctDNA)和 miRNAs 可能在毒性、复发评估和疗效预测中发挥重要作用,并可应用于 CAR-T 疗法的临床应用和建立安全有效的个体化医疗。然而,需要进一步研究以充分了解免疫调节的特定副作用,确定该药物与常规化疗和靶向治疗的最佳顺序和组合,并找到可靠的预测性生物标志物。