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Phase 1 Trials of PNPLA3 siRNA in I148M Homozygous Patients with MAFLD.

作者信息

Fabbrini Elisa, Rady Brian, Koshkina Anastasiya, Jeon Jae Yoon, Ayyar Vivaswath S, Gargano Cynthia, DiProspero Nicholas, Wendel Susan, Hegge Julia, Hamilton Holly, Ding Zhi-Ming, Afrazi Maria, Nicholas Anthony, Pei Tao, Nakano Masayoshi, Ouchi Shohei, Saito Yuki, Yamashita Aimi, Tamamura Ryo, Salazar Hernan, Shapiro Craig, Yoshihara Tatsuya, Yonemura Takuma, Inoue Satoshi, Matsuoka Osamu, Erion Mark, Pocai Alessandro, Makimura Hideo

机构信息

Janssen Research and Development, Raritan, NJ

Janssen Research and Development, Spring House, PA.

出版信息

N Engl J Med. 2024 Aug 1;391(5):475-476. doi: 10.1056/NEJMc2402341.

Abstract
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