少有人走的路：英国呼吸基因治疗联盟在囊性纤维化基因治疗方面稳步前行 - Suppr

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超能文献

The Road Less Traveled: Slow but Steady Progress Toward Cystic Fibrosis Gene Therapy by the UK Respiratory Gene Therapy Consortium.

作者信息

Flotte Terence R

机构信息

Horae Gene Therapy Center University of Massachusetts Chan Medical School Worcester, Massachusetts.

出版信息

Am J Respir Crit Care Med. 2024 Dec 15;210(12):1387-1389. doi: 10.1164/rccm.202408-1516ED.

DOI:10.1164/rccm.202408-1516ED

PMID:39265185

原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC11716029/

Abstract

摘要

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/adde/11716029/44de708f7de1/rccm.202408-1516EDf1.jpg

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Am J Respir Crit Care Med. 2024 Dec 15;210(12):1398-1408. doi: 10.1164/rccm.202402-0389CI.

A Paradox of the Field's Own Success: Unintended Challenges in Bringing Cutting-Edge Science from the Bench to the Market.该领域自身成功带来的悖论：将前沿科学从实验室推向市场过程中意想不到的挑战。

Hum Gene Ther. 2024 Feb;35(3-4):83-88. doi: 10.1089/hum.2023.29264.nyi.

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis.针对囊性纤维化患者的首次人体慢病毒试验的准备工作。

Thorax. 2017 Feb;72(2):137-147. doi: 10.1136/thoraxjnl-2016-208406. Epub 2016 Nov 16.

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Lancet Respir Med. 2015 Sep;3(9):684-691. doi: 10.1016/S2213-2600(15)00245-3. Epub 2015 Jul 3.

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