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Eltrombopag in chronic myelomonocytic leukemia with severe thrombocytopenia. A Groupe Francophone des Myélodysplasies (GFM) study.

作者信息

Rabian Florence, Chevret Sylvie, Gruson Bérengère, Thépot Sylvain, Walter-Petrich Anouk, Braun Thorsten, Vey Norbert, Torregrosa-Diaz José Miguel, Peterlin Pierre, Toma Andrea, D'Aveni Maud, Delaunay Jacques, Legros Laurence, Droin Nathalie, Chermat Fatiha, Lusina Daniel, Adès Lionel, Sapena Rosa, Solary Eric, Fenaux Pierre, Itzykson Raphael

机构信息

Hematology Department, Hôpital Saint-Louis, Assistance Publique-Hôpitaux de Paris, F-75010, Paris, France.

SBIM, APHP, Hôpital Saint-Louis, INSERM, UMR-1153, ECSTRRA Team, Paris, France.

出版信息

Leukemia. 2024 Nov;38(11):2510-2513. doi: 10.1038/s41375-024-02402-8. Epub 2024 Sep 12.

DOI:10.1038/s41375-024-02402-8
PMID:39266637
Abstract
摘要

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Eltrombopag for Low-Risk Myelodysplastic Syndromes With Thrombocytopenia: Interim Results of a Phase II, Randomized, Placebo-Controlled Clinical Trial (EQOL-MDS).依鲁替尼治疗血小板减少性低危骨髓增生异常综合征的疗效:一项 II 期、随机、安慰剂对照临床试验(EQOL-MDS)的中期结果。
J Clin Oncol. 2023 Oct 1;41(28):4486-4496. doi: 10.1200/JCO.22.02699. Epub 2023 Jun 9.
2
Eltrombopag for myelodysplastic syndromes or chronic myelomonocytic leukaemia with no excess blasts and thrombocytopenia: a French multicentre retrospective real-life study.Eltrombopag 治疗不伴有原始细胞增多的骨髓增生异常综合征或慢性粒单核细胞白血病伴血小板减少:一项法国多中心回顾性真实世界研究。
Br J Haematol. 2021 Jul;194(2):336-343. doi: 10.1111/bjh.17539. Epub 2021 Jun 20.
3
Clinical spectrum, outcome and management of immune thrombocytopenia associated with myelodysplastic syndromes and chronic myelomonocytic leukemia.
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Haematologica. 2021 May 1;106(5):1414-1422. doi: 10.3324/haematol.2020.272559.
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