监管者，准备好。
Regulators, mount up.
机构信息
Department of Genetics, Stanford University School of Medicine, Stanford, CA, USA.
出版信息
Science. 2024 Oct 4;386(6717):24-25. doi: 10.1126/science.ads5951. Epub 2024 Oct 3.
PMID:39361768
Abstract
Cryptic exons enable delivery of therapies only to sick neurons in a motor neuron disease.
摘要
隐秘外显子使疗法只能递送到运动神经元疾病中病态神经元。
Zotero 插件