Mitochondrial Biology and Neurodegeneration Unit, Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD, 20892, USA.
Bioinformatics Core, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD, 20892, USA.
EMBO J. 2024 Nov;43(22):5548-5585. doi: 10.1038/s44318-024-00242-x. Epub 2024 Oct 8.
Mitochondrial dysfunction causes devastating disorders, including mitochondrial myopathy, but how muscle senses and adapts to mitochondrial dysfunction is not well understood. Here, we used diverse mouse models of mitochondrial myopathy to show that the signal for mitochondrial dysfunction originates within mitochondria. The mitochondrial proteins OMA1 and DELE1 sensed disruption of the inner mitochondrial membrane and, in response, activated the mitochondrial integrated stress response (mt-ISR) to increase the building blocks for protein synthesis. In the absence of the mt-ISR, protein synthesis in muscle was dysregulated causing protein misfolding, and mice with early-onset mitochondrial myopathy failed to grow and survive. The mt-ISR was similar following disruptions in mtDNA maintenance (Tfam knockout) and mitochondrial protein misfolding (CHCHD10 G58R and S59L knockin) but heterogenous among mitochondria-rich tissues, with broad gene expression changes observed in heart and skeletal muscle and limited changes observed in liver and brown adipose tissue. Taken together, our findings identify that the DELE1 mt-ISR mediates a similar response to diverse forms of mitochondrial stress and is critical for maintaining growth and survival in early-onset mitochondrial myopathy.
线粒体功能障碍会导致毁灭性疾病,包括线粒体肌病,但肌肉如何感知和适应线粒体功能障碍还不太清楚。在这里,我们使用多种线粒体肌病的小鼠模型表明,线粒体功能障碍的信号源自线粒体内部。线粒体蛋白 OMA1 和 DELE1 感知到线粒体内膜的破坏,并对此做出反应,激活线粒体整合应激反应(mt-ISR),增加蛋白质合成的构建块。如果没有 mt-ISR,肌肉中的蛋白质合成就会失调,导致蛋白质错误折叠,并且患有早发性线粒体肌病的小鼠无法生长和存活。在 mtDNA 维持(Tfam 敲除)和线粒体蛋白错误折叠(CHCHD10 G58R 和 S59L 定点突变)中断后,mt-ISR 是相似的,但在富含线粒体的组织中存在异质性,在心脏和骨骼肌中观察到广泛的基因表达变化,而在肝脏和棕色脂肪组织中观察到的变化有限。总之,我们的研究结果表明,DELE1 mt-ISR 介导了对多种形式的线粒体应激的相似反应,对于维持早发性线粒体肌病的生长和存活至关重要。