CRISPR-Cas9-directed gene therapy for spinocerebellar ataxia type 1.
作者信息
Miclăuș Mihai, Balmus Gabriel
机构信息
UK Dementia Research Institute at the University of Cambridge, Cambridge CB2 0AH, UK.
Department of Molecular Neuroscience, Transylvanian Institute of Neuroscience, 400191 Cluj-Napoca, Romania.
出版信息
Mol Ther Nucleic Acids. 2024 Nov 14;35(4):102377. doi: 10.1016/j.omtn.2024.102377. eCollection 2024 Dec 10.
Abstract
摘要
Zotero 插件