Olarewaju Bukola A, Alexander Erin R, Crowe Monica M, Dandurand Kristina, Melville David, Shamoun Fadi, Osundiji Mayowa A
School of Science and Engineering, University of Dundee, Dundee, DD1 4HN, UK.
Department of Clinical Genomics, Mayo Clinic, 13400 East Shea Blvd, Scottsdale, AZ, 85259, USA.
Skeletal Radiol. 2025 Jul;54(7):1537-1541. doi: 10.1007/s00256-024-04852-8. Epub 2024 Dec 5.
COL9A1 encodes the alpha-1 chain of type IX collagen heterotrimer, which is a vital component of collagen fibrils in hyaline cartilage. There are preliminary lines of evidence suggesting that COL9A1 mutations may be associated with autosomal dominant multiple epiphyseal dysplasia (MED), a disorder affecting the epiphysis of long bones. With only 2 reported cases (both from the same family) of MED in autosomal dominant COL9A1-related disorders (MIM 614135) in the clinical scientific literature hitherto, the phenotype is poorly understood at present. Here, we report the clinical and imaging findings associated with a novel COL9A1 mutation in comparison to the previously reported cases. We studied a 22-year-old male, who presented with a chronic history of leg pain and laxity of the knee joint, in the context of a history of pectus carinatum requiring a chest brace, and tall stature (height = 186.9 cm) with bilateral piezogenic pedal papules. Gene panel testing and a radiographic skeletal survey were subsequently performed. Gene panel test showed a heterozygous pathogenic variant in the COL9A1 that is denoted as c.188del (p.Phe63Serfs*3) and is predicted to result in a loss-of-function. The patient's long bones all appeared slender on a radiograph, without apparent epiphyseal dysplasia. Our findings suggest that the phenotypic spectrum of COL9A1-related disorders may potentially include other skeletal anomalies (such as pectus carinatum and slender appearance of long bones) aside from epiphyseal dysplasia.
COL9A1基因编码IX型胶原三聚体的α-1链,它是透明软骨中胶原纤维的重要组成部分。有初步证据表明,COL9A1基因突变可能与常染色体显性多发性骨骺发育不良(MED)有关,这是一种影响长骨骨骺的疾病。迄今为止,临床科学文献中仅报道了2例(均来自同一家族)常染色体显性COL9A1相关疾病(MIM 614135)中的MED病例,目前对其表型了解甚少。在此,我们报告与一个新的COL9A1突变相关的临床和影像学发现,并与先前报道的病例进行比较。我们研究了一名22岁男性,他有慢性腿痛和膝关节松弛的病史,同时有鸡胸病史需要佩戴胸带,身材高大(身高 = 186.9厘米),双侧有压迫性足部丘疹。随后进行了基因检测和骨骼X线检查。基因检测显示COL9A1基因存在一个杂合性致病变异,记为c.188del(p.Phe63Serfs*3),预计会导致功能丧失。在X线片上,患者的所有长骨均显得细长,无明显骨骺发育异常。我们的研究结果表明,COL9A1相关疾病的表型谱除了骨骺发育异常外,可能还包括其他骨骼异常(如鸡胸和长骨细长外观)。