Uytterhoeven Valerie, Verstreken Patrik, Nachman Eliana
Vlaams Instituut voor Biotechnologie Center for Brain and Disease Research , Leuven, Belgium.
Department of Neurosciences, Leuven Brain Institute, KU Leuven, Leuven, Belgium.
J Cell Biol. 2025 Feb 3;224(2). doi: 10.1083/jcb.202409104. Epub 2024 Dec 24.
Synaptic dysfunction is one of the earliest cellular defects observed in Alzheimer's disease (AD) and Parkinson's disease (PD), occurring before widespread protein aggregation, neuronal loss, and cognitive decline. While the field has focused on the aggregation of Tau and α-Synuclein (α-Syn), emerging evidence suggests that these proteins may drive presynaptic pathology even before their aggregation. Therefore, understanding the mechanisms by which Tau and α-Syn affect presynaptic terminals offers an opportunity for developing innovative therapeutics aimed at preserving synapses and potentially halting neurodegeneration. This review focuses on the molecular defects that converge on presynaptic dysfunction caused by Tau and α-Syn. Both proteins have physiological roles in synapses. However, during disease, they acquire abnormal functions due to aberrant interactions and mislocalization. We provide an overview of current research on different essential presynaptic pathways influenced by Tau and α-Syn. Finally, we highlight promising therapeutic targets aimed at maintaining synaptic function in both tauopathies and synucleinopathies.
突触功能障碍是在阿尔茨海默病(AD)和帕金森病(PD)中观察到的最早的细胞缺陷之一,发生在广泛的蛋白质聚集、神经元丢失和认知衰退之前。虽然该领域一直专注于 Tau 蛋白和 α-突触核蛋白(α-Syn)的聚集,但新出现的证据表明,这些蛋白质甚至在聚集之前就可能导致突触前病理变化。因此,了解 Tau 蛋白和 α-Syn 影响突触前终末的机制,为开发旨在保护突触并可能阻止神经退行性变的创新疗法提供了机会。本综述重点关注导致 Tau 蛋白和 α-Syn 引起突触前功能障碍的分子缺陷。这两种蛋白质在突触中都具有生理作用。然而,在疾病过程中,由于异常相互作用和定位错误,它们获得了异常功能。我们概述了目前关于受 Tau 蛋白和 α-Syn 影响的不同重要突触前途径的研究。最后,我们强调了旨在维持 Tau 蛋白病和突触核蛋白病中突触功能的有前景的治疗靶点。