Ma Yitao, Kaminski Matthew, Crutcher Robert
Department of Neurology, Walter Reed National Military Medical Center, Bethesda, MD, 20889, USA.
University of Maryland, College Park, MD, 20742, USA.
Neurol Sci. 2025 Apr;46(4):1565-1572. doi: 10.1007/s10072-024-07942-6. Epub 2024 Dec 26.
The effect of felbamate (FBM) on genetic generalized epilepsy (GGE) remains largely unknown. The utilization of FBM has been limited due to its potential risk of aplastic anemia and hepatic failure. This study aimed to comprehensively evaluate the efficacy and safety of FBM in the treatment of drug-resistant GGE.
We searched the databases, including PubMed, Web of Science, Embase, and Google Scholar, to identify cases of GGE treated with FBM. Data on outcomes and adverse events were extracted from these studies.
The literature search yielded 9 studies with 166 cases in which FBM was used as an adjunct therapy to treat drug-resistant GGE. The pooled responder rate to FBM was 65% (95% confidence interval CI, 51-80). 17% (95% CI, 3-31) achieved seizure freedom. 81% (95% CI, 60-100) of patients with Epilepsy with myoclonic atonic seizures were responders. Adverse events were reported in 40% (95% CI, 26-54) of patients.
Patients with drug-resistant GGE achieved good responses to FBM. The high heterogeneity between studies calls for further research with large-scale, randomized controlled trials. Given the rare reports of idiosyncratic reactions of aplastic anemia and hepatic failure, intense laboratory monitoring and a slower titration schedule are recommended.
非氨酯(FBM)对遗传性全身性癫痫(GGE)的影响在很大程度上仍不清楚。由于其存在再生障碍性贫血和肝衰竭的潜在风险,非氨酯的应用受到限制。本研究旨在全面评估非氨酯治疗耐药性GGE的疗效和安全性。
我们检索了包括PubMed、科学网、Embase和谷歌学术在内的数据库,以确定接受非氨酯治疗的GGE病例。从这些研究中提取有关结局和不良事件的数据。
文献检索得到9项研究,共166例,其中非氨酯用作辅助治疗耐药性GGE。非氨酯的合并缓解率为65%(95%置信区间CI,51 - 80)。17%(95%CI,3 - 31)实现无癫痫发作。肌阵挛失张力发作型癫痫患者中有81%(95%CI,60 - 100)为缓解者。40%(95%CI,26 - 54)的患者报告有不良事件。
耐药性GGE患者对非氨酯反应良好。研究之间的高度异质性需要进一步开展大规模随机对照试验。鉴于再生障碍性贫血和肝衰竭等特异反应的报告罕见,建议加强实验室监测并采用更缓慢的滴定方案。