Raman Vishnu, Hall Christopher L, Wetherby Victoria E, Whitney Samantha A, Van Dessel Nele, Forbes Neil S
Department of Chemical Engineering, University of Massachusetts, Amherst, Amherst, MA 01003, USA; Ernest Pharmaceuticals, Inc., Hadley, MA 01035, USA.
Ernest Pharmaceuticals, Inc., Hadley, MA 01035, USA.
Mol Ther. 2025 Feb 5;33(2):649-669. doi: 10.1016/j.ymthe.2024.12.038. Epub 2024 Dec 31.
Effectively targeting intracellular pathways in cancers requires a system that specifically delivers to tumors and internalizes into cancer cells. To achieve this goal, we developed intracellular-delivering (ID) Salmonella with controllable expression of flhDC to regulate flagella production and cell invasion. We hypothesized that controlling flhDC would overcome the poor colonization seen in prior clinical trials. To test this hypothesis, we incorporated the aspirin-responsive Psal promoter and tuned flhDC expression with ssra degradation tags. In tumor-bearing mice, controlling flhDC increased protein release, tissue dispersion, and tumor colonization more than 10 million times. We discovered that inducing flhDC increases escape from intracellular vacuoles; however, deleting sseJ prevented escape and further increased protein delivery. Delivering constitutively active caspase-3 with ID-f-s Salmonella (ΔsseJ and induced Psal-flhDC) induced cell death in pancreatic, breast, and liver cancer cells and reduced the growth of breast tumors. This clinically ready strain preferentially colonized metastatic breast tissue 280 and 800 times more than surrounding healthy tissue in the lung and liver, respectively. By precisely controlling tumor colonization and cell invasion, this strain overcomes critical limitations of bacterial therapy and will enable treatment of many hard-to-treat cancers.
有效靶向癌症中的细胞内信号通路需要一个能够特异性递送至肿瘤并内化进入癌细胞的系统。为实现这一目标,我们开发了细胞内递送(ID)沙门氏菌,其flhDC表达可控,以调节鞭毛产生和细胞侵袭。我们假设控制flhDC将克服先前临床试验中观察到的定植不佳问题。为验证这一假设,我们引入了阿司匹林反应性Psal启动子,并通过ssra降解标签调节flhDC表达。在荷瘤小鼠中,控制flhDC使蛋白质释放、组织扩散和肿瘤定植增加了超过1000万倍。我们发现诱导flhDC可增加从细胞内液泡的逃逸;然而,缺失sseJ可阻止逃逸并进一步增加蛋白质递送。用ID-f-s沙门氏菌(ΔsseJ和诱导的Psal-flhDC)递送组成型活性半胱天冬酶-3可诱导胰腺、乳腺和肝癌细胞死亡,并减少乳腺肿瘤的生长。这种临床可用菌株在肺和肝中分别优先定殖于转移性乳腺组织,其定殖量分别是周围健康组织的280倍和800倍。通过精确控制肿瘤定植和细胞侵袭,该菌株克服了细菌疗法的关键局限性,并将能够治疗许多难以治疗的癌症。