Park Se Jun, Shin Kabsoo, Kim In-Ho, Lee MyungAh, Hong Tae Ho, Kim Hyunho
Division of Medical Oncology, Department of Internal Medicine, Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, 222 Banpo-daero, Secho-gu, Seoul, Korea.
Cancer Research Institute, College of Medicine, The Catholic University of Korea, 222 Banpo-daero, Secho-gu, Seoul, Korea.
Sci Rep. 2025 Jan 27;15(1):3386. doi: 10.1038/s41598-025-86523-9.
Advanced hepatocellular carcinoma (HCC) poses treatment challenges, especially where access to multi-kinase inhibitors and ICIs is limited by high costs and lack of insurance. This study evaluates the effectiveness of 5-fluorouracil (5-FU) plus platinum-based chemotherapy as an alternative systemic treatment for advanced HCC. A retrospective analysis of advanced HCC patients treated with 5-FU plus platinum-based chemotherapy was conducted. The Kaplan-Meier method determined median progression-free survival (PFS) and overall survival (OS). From April 2009 to October 2023, 48 patients with advanced HCC were included in the study. Nearly all patients (97.9%) had extrahepatic metastasis and stable liver function, with three-quarters previously treated with sorafenib. At a median follow-up of 7.8 months, the median PFS was 4.2 months (95% CI, 1.3-7.1), and the median OS was 8.2 months (95% CI, 2.5-13.9). A high pretreatment neutrophil-to-lymphocyte ratio (≥ 3.0) adversely affected both PFS (HR = 1.79; 95% CI, 0.99-3.25; p = 0.034) and OS (HR = 2.02; 95% CI, 1.10-3.69; p = 0.011). Hematologic toxicities related to the treatment were substantial, with 62.5% of patients experiencing grade 3 or 4 events, primarily neutropenia, which affected 60.4% of them. Our findings suggest that 5-FU combined with platinum-based chemotherapy is a viable, cost-effective alternative for advanced HCC treatment in resource-limited settings, particularly compared to ICIs and multi-kinase inhibitors, with significant implications for developing countries.
晚期肝细胞癌(HCC)带来了治疗挑战,尤其是在多激酶抑制剂和免疫检查点抑制剂(ICI)因成本高昂且缺乏保险覆盖而难以获得的情况下。本研究评估了5-氟尿嘧啶(5-FU)联合铂类化疗作为晚期HCC替代全身治疗的有效性。对接受5-FU联合铂类化疗的晚期HCC患者进行了回顾性分析。采用Kaplan-Meier法确定中位无进展生存期(PFS)和总生存期(OS)。从2009年4月至2023年10月,48例晚期HCC患者纳入本研究。几乎所有患者(97.9%)都有肝外转移且肝功能稳定,四分之三的患者先前接受过索拉非尼治疗。中位随访7.8个月时,中位PFS为4.2个月(95%CI,1.3 - 7.1),中位OS为8.2个月(95%CI,2.5 - 13.9)。治疗前中性粒细胞与淋巴细胞比值高(≥3.0)对PFS(HR = 1.79;95%CI,0.99 - 3.25;p = 0.034)和OS(HR = 2.02;95%CI,1.10 - 3.69;p = 0.011)均有不利影响。与治疗相关的血液学毒性较为严重,62.5%的患者发生3级或4级事件,主要是中性粒细胞减少,其中60.4%的患者受此影响。我们的研究结果表明,在资源有限的环境中,5-FU联合铂类化疗是晚期HCC治疗的一种可行且具有成本效益的替代方案,特别是与ICI和多激酶抑制剂相比,对发展中国家具有重要意义。