Levacetylleucine (N-acetyl-l-leucine) for Niemann-Pick disease type C.
作者信息
van Gool Raquel, Al-Hertani Walla, Bodamer Olaf, Upadhyay Jaymin
机构信息
Department of Anesthesiology, Critical Care, and Pain Medicine, Boston Children's Hospital, Harvard Medical School, 300 Longwood Ave, Boston, MA, USA; Department of Neurology, Mental Health, and Neuroscience Research Institute, Maastricht University, Universiteitssingel 60, Maastricht, Limburg, The Netherlands.
Division of Metabolic Disorders, Children's Hospital of Orange County, Rady Children's Health, 1201 W. La Veta Ave, Orange, CA, USA.
出版信息
Trends Pharmacol Sci. 2025 Apr;46(4):386-387. doi: 10.1016/j.tips.2025.02.003. Epub 2025 Mar 6.
PMID:40055076
Abstract
摘要
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