Scotti Celeste, Aiuti Alessandro, Naldini Luigi
Fondazione Telethon, Rome, Italy.
San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Nat Rev Genet. 2025 Jul;26(7):437-438. doi: 10.1038/s41576-025-00827-0.