Tremblay-McGaw Alexandra G, Hamlat Elissa J, Becker Natalie C, Astudillo Maya Daniela A, Krystal Andrew D, Sellers Kristin K
Department of Psychiatry and Behavioral Sciences, University of California, San Francisco, San Francisco, CA, United States.
Weill Institute for Neurosciences, University of California, San Francisco, San Francisco, CA, United States.
Front Hum Neurosci. 2025 Apr 16;19:1572972. doi: 10.3389/fnhum.2025.1572972. eCollection 2025.
Deep brain stimulation (DBS) is well suited to target disorders with network dysregulation, as is the case in many neuropsychiatric diseases. While DBS is a well-established therapy for Parkinson's disease, essential tremor, dystonia, and medically refractory epilepsy, it is actively being studied in clinical trials for neuropsychiatric disorders including treatment-refractory major depressive disorder (MDD). Due to the nature of symptomology and participant characteristics, special care must be taken in the design and implementation of clinical trials testing DBS for neuropsychiatric disorders. In particular, these studies typically include multi-year relationships between participants and study staff with frequent interactions, high burden of study activities on participants, and disclosure by participants of sensitive information related to symptoms and disease state. Through our experience with six participants across more than 5 years of the Presidio clinical trial assessing personalized closed-loop DBS for treatment-refractory MDD, we have gathered experience and evidence to inform best practices for conducting these interaction-intensive clinical studies in a vulnerable population. Here, we present these Key Practices along with discussion, informed by multiple fundamental principles: The Belmont Report; emotional and physical safety for study participants and staff; and integrity and validity of scientific outcomes.
深部脑刺激(DBS)非常适合针对网络失调的疾病,许多神经精神疾病就是这种情况。虽然DBS是治疗帕金森病、特发性震颤、肌张力障碍和药物难治性癫痫的成熟疗法,但目前正在针对包括难治性重度抑郁症(MDD)在内的神经精神疾病进行积极的临床试验研究。由于症状学和参与者特征的性质,在设计和实施针对神经精神疾病的DBS临床试验时必须格外小心。特别是,这些研究通常包括参与者与研究人员之间持续多年的关系,频繁的互动,参与者承担的研究活动负担较重,以及参与者披露与症状和疾病状态相关的敏感信息。通过我们在为期5年多的Presidio临床试验中对6名参与者进行的评估个性化闭环DBS治疗难治性MDD的经验,我们积累了经验和证据,为在弱势群体中开展这些互动密集型临床研究的最佳实践提供参考。在此,我们结合多个基本原则的讨论,介绍这些关键实践:《贝尔蒙报告》;研究参与者和工作人员的情感与身体安全;以及科学结果的完整性和有效性。