Dada Sarah, Akbari Vahid, Hejla Duha, Shen Yaoqing, Dixon Katherine, Choufani Sanaa, Weksberg Rosanna A, Boerkoel Cornelius F, Stewart Laura, Schlade-Bartusiak Kamilla, Strong Emma, Fox Danya, Gamu Daniel, Gibson William T, Jones Steven J M
Canada's Michael Smith Genome Sciences Centre, BC Cancer, Vancouver, British Columbia, Canada.
Bioinformatics Graduate Program, University of British Columbia, Vancouver, British Columbia, Canada.
J Med Genet. 2025 Jul 21;62(8):502-507. doi: 10.1136/jmg-2024-110262.
Temple syndrome is an imprinting disorder resulting from abnormal genomic or epigenomic aberrations of chromosome 14 including maternal uniparental disomy (matUPD), paternal deletion of 14q32, or aberrant methylation of the imprinting control regions at 14q32. Understanding the underlying molecular mechanism is essential to understanding the recurrence risk and physical effects. Currently, diagnosis requires the detection of aberrant methylation and copy number loss via methylation-sensitive assays such as methylation-specific multiplex ligation-dependent probe amplification, and short tandem repeat analysis to detect matUPD and the presence of epimutation. Therefore, a one-step approach that can detect aberrant methylation and underlying genetic mechanisms would be of high clinical value. Here we use nanopore sequencing to delineate the molecular diagnosis of a case with Temple syndrome. We demonstrate the application of nanopore sequencing to detect aberrant methylation and underlying genetic mechanisms simultaneously in this case, thus providing a proof of concept for a one-step approach for molecular diagnosis of this disorder.
坦普尔综合征是一种印记障碍,由14号染色体的基因组或表观基因组异常引起,包括母源性单亲二体(matUPD)、14q32的父源缺失或14q32印记控制区域的异常甲基化。了解潜在的分子机制对于理解复发风险和身体影响至关重要。目前,诊断需要通过甲基化敏感检测方法,如甲基化特异性多重连接依赖探针扩增,以及短串联重复序列分析来检测matUPD和表观突变的存在,以检测异常甲基化和拷贝数丢失。因此,一种能够检测异常甲基化和潜在遗传机制的一步法将具有很高的临床价值。在此,我们使用纳米孔测序来阐述一例坦普尔综合征病例的分子诊断。我们证明了在该病例中纳米孔测序可同时检测异常甲基化和潜在遗传机制,从而为该疾病的分子诊断一步法提供了概念验证。