Phung Quan H, Tsai Alexander K, Park Byoung U, Schat Robben, Spong Richard, Tsai L Jill, Kulkarni Amit A, Antonarakis Emmanuel S, Gupta Arjun
University of Minnesota, Minneapolis, MN, United States.
Guardant Health, Palo Alto, CA, United States.
Front Oncol. 2025 Jun 12;15:1579364. doi: 10.3389/fonc.2025.1579364. eCollection 2025.
We present a case of a 65-year-old woman with a history of kidney and pancreas transplants for type 1 diabetes mellitus who presented with small bowel obstruction and was found to have a poorly differentiated small bowel adenocarcinoma with multifocal osseous and nodal metastases. Plasma-based next generation circulating tumor deoxyribonucleic acid (DNA) sequencing revealed mismatch repair deficiency and an exceptionally high tumor mutational burden (TMB) of 1069 mutations/megabase (mut/Mb). Initial management consisted of cytotoxic chemotherapy (FOLFOX; 5-fluorouracil, leucovorin, and oxaliplatin) given the urgent need for a clinical response. Following multidisciplinary discussion and shared decision-making, nivolumab was added with cycle 3 of FOLFOX. Transplant-related immunosuppression was adjusted, and pancreas and kidney transplant function were monitored closely. Potential organ rejection was monitored using donor-derived cell-free DNA. Immune-related adverse events were not observed. After 5 cycles of treatment (3 cycles involving nivolumab), she achieved a complete clinical, molecular, and radiographic response. There was minimal evidence of allograft rejection without signs of dysfunction. Treatment was discontinued and subsequent surveillance imaging suggested durable remission for at least 9 months following treatment cessation. This case highlights the importance of genomic testing and targeting actionable molecular alterations in patients with rare cancers, as well as the role of multidisciplinary care.
我们报告了一例65岁女性病例,该患者有1型糖尿病史,接受过肾脏和胰腺移植,因小肠梗阻就诊,被发现患有低分化小肠腺癌,伴有多灶性骨转移和淋巴结转移。基于血浆的下一代循环肿瘤脱氧核糖核酸(DNA)测序显示错配修复缺陷,肿瘤突变负荷(TMB)异常高,为1069个突变/兆碱基(mut/Mb)。鉴于迫切需要临床反应,初始治疗方案为细胞毒性化疗(FOLFOX;5-氟尿嘧啶、亚叶酸钙和奥沙利铂)。经过多学科讨论和共同决策,在FOLFOX第3周期时加用纳武单抗。调整了与移植相关的免疫抑制,并密切监测胰腺和肾脏移植功能。使用供体来源的游离DNA监测潜在的器官排斥反应。未观察到免疫相关不良事件。经过5个周期的治疗(3个周期使用纳武单抗),她在临床、分子和影像学上均取得了完全缓解。几乎没有同种异体移植排斥的证据,也没有功能障碍的迹象。治疗停止,随后的监测成像显示在治疗停止后至少9个月病情持续缓解。该病例突出了基因组检测和针对罕见癌症患者可操作分子改变进行靶向治疗的重要性,以及多学科护理的作用。