Liu Junyu, Wang Hua, Zhang Caihua
Shandong Ruixin Pharmaceutical Company, Intersection of Tengfei East Road and East Second Ring Road, Yishui County, Linyi, Shandong Province 276400, China.
Shandong Luoxin Pharmaceutical Group Stock Company, Luoqi Road, Luozhuang County, Linyi, Shandong Province 276017, China.
J Leukoc Biol. 2025 Jul 9;117(7). doi: 10.1093/jleuko/qiaf083.
MicroRNA-93 (miR-93) has been implicated in the pathogenesis of myelodysplastic syndrome (MDS), though its precise role in the regulation of hematopoiesis and cell fate in MDS remains poorly understood. This study aimed to investigate the impact of miR-93 on cell proliferation, apoptosis, and hematopoiesis in MDS, focusing on the PAG1-mediated EGFR signaling pathway. Bioinformatic analyses were used to identify the miR-93-PAG1-EGFR axis in MDS. Gain- and loss-of-function experiments were performed using miR-93 mimics, miR-93 inhibitors, and siRNA targeting PAG1 to evaluate their roles in MDS progression. Bone marrow mononuclear cells from MDS patients were analyzed to assess the molecular expression patterns. Our findings revealed elevated miR-93 expression and reduced PAG1 levels, alongside activation of the EGFR signaling pathway in MDS patient samples. Downregulation of miR-93 or activation of PAG1 reversed these molecular alterations. Specifically, reduced miR-93 levels led to decreased EGFR phosphorylation and upregulation of PAG1 expression, which resulted in suppressed MDS cell proliferation, increased apoptosis, and enhanced hematopoiesis. Furthermore, the expression of key signaling molecules, including c-fos, TNF-α, IL-3, and stem cell factor (SCF), was modulated in response to miR-93 or PAG1 regulation. This study demonstrates that downregulation of miR-93 suppresses MDS progression through the inactivation of the EGFR signaling pathway and the upregulation of PAG1. Our results suggest that targeting the miR-93/PAG1/EGFR axis could offer potential therapeutic strategies for managing myelodysplastic syndrome (MDS) and promoting hematopoiesis.
微小RNA-93(miR-93)已被认为与骨髓增生异常综合征(MDS)的发病机制有关,但其在MDS造血调控和细胞命运中的精确作用仍知之甚少。本研究旨在探讨miR-93对MDS细胞增殖、凋亡和造血的影响,重点关注PAG1介导的EGFR信号通路。采用生物信息学分析来确定MDS中的miR-93-PAG1-EGFR轴。使用miR-93模拟物、miR-93抑制剂和靶向PAG1的小干扰RNA(siRNA)进行功能获得和功能缺失实验,以评估它们在MDS进展中的作用。对MDS患者的骨髓单个核细胞进行分析,以评估分子表达模式。我们的研究结果显示,MDS患者样本中miR-93表达升高、PAG1水平降低,同时EGFR信号通路激活。miR-93的下调或PAG1的激活可逆转这些分子改变。具体而言,miR-93水平降低导致EGFR磷酸化减少和PAG1表达上调,进而抑制MDS细胞增殖、增加细胞凋亡并增强造血功能。此外,关键信号分子,包括c-fos、肿瘤坏死因子-α(TNF-α)、白细胞介素-3(IL-3)和干细胞因子(SCF)的表达,会因miR-93或PAG1的调控而发生变化。本研究表明,miR-93的下调通过使EGFR信号通路失活和上调PAG1来抑制MDS进展。我们的结果表明,靶向miR-93/PAG1/EGFR轴可为治疗骨髓增生异常综合征(MDS)和促进造血提供潜在的治疗策略。