Yadav Sumeet K, Joshi Utsav, Hussein Guleid, Warsame Mohamed, Liu Bolun, Shrestha Abhash, Krastev Peter, Korsapati Hariprasad Reddy, Singh Amrit
Hospital Internal Medicine, Mayo Clinic Health System, Mankato, MN 56001, USA.
Hematology and Medical Oncology Fellowship Program, Moffitt Cancer Center, Tampa, FL 33612, USA.
Cancers (Basel). 2025 Aug 28;17(17):2824. doi: 10.3390/cancers17172824.
Acute myeloid leukemia (AML) is an aggressive hematologic malignancy characterized by the clonal proliferation of myeloid precursors and rapid progression. Historically consisting of intensive chemotherapy, AML management has evolved significantly due to advances in molecular diagnostics and risk stratification. This review discusses current therapeutic paradigms in AML, emphasizing the growing role of personalized medicine across age and risk groups. For younger, fit patients, intensive regimens such as the "7 + 3" protocol remain the standard, often enhanced by targeted agents like FMS-like tyrosine kinase 3 (FLT3) and IDH inhibitors. Older or unfit individuals benefit from low-intensity treatments such as hypomethylating agents combined with venetoclax, now considered a frontline standard of care. The use of liposomal chemotherapy (CPX-351), measurable residual disease (MRD) monitoring, and maintenance therapy further refine post-remission strategies. Emerging therapies, including menin inhibitors, antibody-drug conjugates, and immunotherapies like CAR-T cells and vaccines, offer additional options, especially in relapsed/refractory settings. This comprehensive review outlines the current landscape and future directions in AML therapy, emphasizing the transition toward individualized, mutation-driven treatment strategies.
急性髓系白血病(AML)是一种侵袭性血液系统恶性肿瘤,其特征为髓系前体细胞的克隆性增殖和快速进展。历史上AML的治疗主要是强化化疗,由于分子诊断和风险分层技术的进步,AML的治疗模式已发生显著演变。本综述讨论了AML当前的治疗模式,强调了个性化医疗在不同年龄和风险组中日益重要的作用。对于年轻、身体状况良好的患者,诸如“7 + 3”方案等强化治疗方案仍是标准治疗,通常还会联合使用FMS样酪氨酸激酶3(FLT3)抑制剂和异柠檬酸脱氢酶(IDH)抑制剂等靶向药物来增强疗效。年龄较大或身体状况不佳的患者则受益于低强度治疗,如去甲基化药物联合维奈克拉,目前这被视为一线标准治疗方案。脂质体化疗(CPX - 351)的应用、可测量残留病(MRD)监测以及维持治疗进一步优化了缓解后治疗策略。新兴疗法,包括Menin抑制剂、抗体药物偶联物以及嵌合抗原受体T细胞(CAR - T)和疫苗等免疫疗法,提供了更多选择,尤其是在复发/难治性AML的治疗中。这篇全面综述概述了AML治疗的当前格局和未来方向,强调了向个体化、突变驱动治疗策略的转变。