Kozlowski M, Mlinaric-Rascan I, Feng G S, Shen R, Pawson T, Siminovitch K A
Department of Medicine, University of Toronto, Ontario, Canada.
J Exp Med. 1993 Dec 1;178(6):2157-63. doi: 10.1084/jem.178.6.2157.
Mutations in the gene encoding the phosphotyrosine phosphatase PTP1C, a cytoplasmic protein containing a COOH-terminal catalytic and two NH2-terminal Src homology 2 (SH2) domains, have been identified in motheaten (me) and viable motheaten (mev) mice and are associated with severe hemopoietic dysregulation. The me mutation is predicted to result in termination of the PTP1C polypeptide within the first SH2 domain, whereas the mev mutation creates an insertion or deletion in the phosphatase domain. No PTP1C RNA or protein could be detected in the hemopoietic tissues of me mice, nor could PTP1C phosphotyrosine phosphatase activity be isolated from cells homozygous for the me mutation. In contrast, mice homozygous for the less severe mev mutation expressed levels of full-length PTP1C protein comparable to those detected in wild type mice and the SH2 domains of mev PTP1C bound normally to phosphotyrosine-containing ligands in vitro. Nevertheless, the mev mutation induced a marked reduction in PTP1C activity. These observations provide strong evidence that the motheaten phenotypic results from loss-of-function mutations in the PTP1C gene and imply a critical role for PTP1C in the regulation of hemopoietic differentiation and immune function.
编码磷酸酪氨酸磷酸酶PTP1C的基因突变已在斑驳病(me)和存活斑驳病(mev)小鼠中被鉴定出来,该基因是一种细胞质蛋白,含有一个COOH末端催化结构域和两个NH2末端Src同源2(SH2)结构域,且与严重的造血失调有关。预计me突变会导致PTP1C多肽在第一个SH2结构域内终止,而mev突变则会在磷酸酶结构域中产生插入或缺失。在me小鼠的造血组织中检测不到PTP1C RNA或蛋白质,从me突变纯合子细胞中也分离不出PTP1C磷酸酪氨酸磷酸酶活性。相比之下,mev突变较轻的纯合子小鼠表达的全长PTP1C蛋白水平与野生型小鼠中检测到的水平相当,并且mev PTP1C的SH2结构域在体外能正常结合含磷酸酪氨酸的配体。然而,mev突变导致PTP1C活性显著降低。这些观察结果提供了强有力的证据,表明斑驳病表型是由PTP1C基因功能丧失突变引起的,并暗示PTP1C在造血分化和免疫功能调节中起关键作用。