Roguska M A, Pedersen J T, Keddy C A, Henry A H, Searle S J, Lambert J M, Goldmacher V S, Blättler W A, Rees A R, Guild B C
ImmunoGen, Inc., Cambridge, MA 02139.
Proc Natl Acad Sci U S A. 1994 Feb 1;91(3):969-73. doi: 10.1073/pnas.91.3.969.
Two murine monoclonal antibodies, N901 (anti-CD56) and anti-B4 (anti-CD19), were humanized by a process we call "resurfacing." A systematic analysis of known antibody structures has been used to determine the relative solvent accessibility distributions of amino acid residues in murine and human antibody variable (Fv) regions and has shown that the sequence alignment positions of surface amino acids for human and murine variable region heavy (VH) and light (VL) chains are conserved with 98% fidelity across species. While the amino acid usage at these surface positions creates surface residue patterns that are conserved within species, there are no identical patterns across species. However, surprisingly few amino acid changes need to be made to convert a murine Fv surface pattern to that characteristic of a human surface. Resurfacing was used to change the patterns of surface accessible residues in the Fv regions of the N901 and anti-B4 antibodies to resemble those found on the Fv regions of human antibody sequences. Two different procedures for selecting a human sequence were compared. For anti-B4, a data base of clonally derived human VL-VH sequence pairs was used, while for N901, sequences for VL and VH were independently selected from the Kabat et al. data base [Kabat, E. A., Wu, T. T., Reid-Miller, M., Perry, H. M. & Gottesman, K. S. (1991) Sequences of Proteins of Immunological Interest (DHHS, Washington, DC), 5th Ed.]. Resurfaced N901 and anti-B4 antibodies had apparent affinities for their cell surface ligands that were identical to those of their respective parent murine antibodies. These data provide evidence that, despite the differences in the surfaces of mouse and human Fv regions, it is possible to substitute one for the other while retaining full antigen binding affinity.
两种鼠源单克隆抗体,N901(抗CD56)和抗B4(抗CD19),通过我们称为“表面重塑”的过程进行人源化。对已知抗体结构进行系统分析,以确定鼠源和人源抗体可变(Fv)区域中氨基酸残基的相对溶剂可及性分布,结果表明,人源和鼠源可变区重链(VH)和轻链(VL)表面氨基酸的序列比对位置在物种间的保守率达98%。虽然这些表面位置的氨基酸使用情况形成了物种内保守的表面残基模式,但物种间不存在相同的模式。然而,令人惊讶的是,将鼠源Fv表面模式转变为人源表面特征所需的氨基酸变化极少。表面重塑被用于改变N901和抗B4抗体Fv区域中表面可及残基的模式,使其类似于人源抗体序列Fv区域中的模式。比较了两种选择人源序列的不同方法。对于抗B4,使用了克隆衍生的人源VL - VH序列对数据库,而对于N901,VL和VH序列是从卡巴特等人的数据库[卡巴特,E.A.,吴,T.T.,里德 - 米勒,M.,佩里,H.M.和戈特斯曼,K.S.(1991年)《具有免疫学意义的蛋白质序列》(美国卫生与公众服务部,华盛顿特区),第5版]中独立选择的。表面重塑后的N901和抗B4抗体对其细胞表面配体的表观亲和力与各自亲本鼠源抗体相同。这些数据证明,尽管小鼠和人源Fv区域表面存在差异,但在保留完全抗原结合亲和力的同时,有可能用一种取代另一种。