Snyderman S E, Sansaricq C, Chen W J, Norton P M, Phansalkar S V
J Pediatr. 1977 Apr;90(4):563-8. doi: 10.1016/s0022-3476(77)80367-3.
The clinical features of argininemia in two cousins included hyperactivity, spasticity, ataxia, retardation, and repeated attacks of hyperammonemia. Study of a large kindred suggests that arginase-deficiency is transmitted as a Mendelian recessive. Treatment with an essential amino acid mixture with the total nitrogen intake limited to the requirement, controlled the hyperammonemia, reduced the plasma arginine level, and permitted a marked clinical improvement. There has been a significant increase in intelligence levels; the previously retarded children are now approaching the normal range of function.
两名表亲的精氨酸血症临床特征包括多动、痉挛、共济失调、发育迟缓以及反复的高氨血症发作。对一个大家族的研究表明,精氨酸酶缺乏症以孟德尔隐性方式遗传。用必需氨基酸混合物进行治疗,同时将总氮摄入量限制在所需水平,可控制高氨血症,降低血浆精氨酸水平,并使临床症状显著改善。智力水平有了显著提高;之前发育迟缓的儿童现在正接近正常功能范围。