Spector E B, Kiernan M, Bernard B, Cederbaum S D
Am J Hum Genet. 1980 Jan;32(1):79-87.
Prenatal diagnosis of inborn errors of metabolism has been possible only if the enzyme affected is expressed in amniotic fluid cells grown in culture. Arginase is essentially undetectable in normal human fibroblasts, amniotic fluid, and amniotic fluid cells but is present in high amounts in red blood cells. It is absent in the red blood cells of patients with liver arginase deficiency. The properties of the enzyme in the red cells of healthy children and adults were compared to those of the enzyme obtained from cord blood red cells of 13--20-week fetuses obtained at hysterotomy. The activities, heavy metal requirements, heat stability, pH optimum, kinetic properties, and reaction with anti-arginase antibody were examined. Both enzyme species were either identical or substantially similar by all criteria. The adult and fetal enzymes are, therefore, probably determined by the same structural gene. Fetal red cells obtained during amniocentesis and amnioscopy should then be a suitable tissue to use to make the prenatal diagnosis of arginase deficiency.
只有当受影响的酶在培养的羊水细胞中表达时,才能对先天性代谢缺陷进行产前诊断。在正常人成纤维细胞、羊水及羊水细胞中基本检测不到精氨酸酶,但在红细胞中含量很高。肝精氨酸酶缺乏症患者的红细胞中则没有精氨酸酶。将健康儿童和成人红细胞中的酶特性与通过剖宫产获得的13 - 20周胎儿脐带血红细胞中的酶特性进行了比较。检测了酶的活性、重金属需求、热稳定性、最适pH值、动力学特性以及与抗精氨酸酶抗体的反应。所有标准下,两种酶均相同或基本相似。因此,成人和胎儿的酶可能由相同的结构基因决定。那么,在羊膜穿刺术和羊膜镜检查期间获得的胎儿红细胞应该是用于精氨酸酶缺乏症产前诊断的合适组织。