Zhang H, Yang Y, Horton J L, Samoilova E B, Judge T A, Turka L A, Wilson J M, Chen Y
Institute for Human Gene Therapy, Department of Molecular and Cellular Engineering, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania 19104, USA.
J Clin Invest. 1997 Oct 15;100(8):1951-7. doi: 10.1172/JCI119726.
Both rheumatoid arthritis and animal models of autoimmune arthritis are characterized by hyperactivation of synovial cells and hyperplasia of the synovial membrane. The activated synovial cells produce inflammatory cytokines and degradative enzymes that lead to destruction of cartilage and bones. Effective treatment of arthritis may require elimination of most or all activated synovial cells. The death factor Fas/Apo-1 and its ligand (FasL) play pivotal roles in maintaining self-tolerance and immune privilege. Fas is expressed constitutively in most tissues, and is dramatically upregulated at the site of inflammation. In both rheumatoid arthritis and animal models of autoimmune arthritis, high levels of Fas are expressed on activated synovial cells and infiltrating leukocytes in the inflamed joints. Unlike Fas, however, the levels of FasL expressed in the arthritic joints are extremely low, and most activated synovial cells survive despite high levels of Fas expression. To upregulate FasL expression in the arthritic joints, we have generated a recombinant replication-defective adenovirus carrying FasL gene; injection of the FasL virus into inflamed joints conferred high levels of FasL expression, induced apoptosis of synovial cells, and ameliorated collagen-induced arthritis in DBA/1 mice. The Fas-ligand virus also inhibited production of interferon-gamma by collagen-specific T cells. Coadministration of Fas-immunoglobulin fusion protein with the Fas-ligand virus prevented these effects, demonstrating the specificity of the Fas-ligand virus. Thus, FasL gene transfer at the site of inflammation effectively ameliorates autoimmune disease.
类风湿性关节炎和自身免疫性关节炎的动物模型均以滑膜细胞的过度活化和滑膜的增生为特征。活化的滑膜细胞产生炎性细胞因子和降解酶,导致软骨和骨骼破坏。关节炎的有效治疗可能需要清除大多数或所有活化的滑膜细胞。死亡因子Fas/Apo-1及其配体(FasL)在维持自身耐受和免疫豁免中起关键作用。Fas在大多数组织中组成性表达,并在炎症部位显著上调。在类风湿性关节炎和自身免疫性关节炎的动物模型中,活化的滑膜细胞和炎症关节中的浸润白细胞均高表达Fas。然而,与Fas不同,关节炎关节中表达的FasL水平极低,尽管Fas表达水平很高,但大多数活化的滑膜细胞仍存活。为了上调关节炎关节中FasL的表达,我们构建了携带FasL基因的重组复制缺陷型腺病毒;将FasL病毒注射到炎症关节中可使FasL高水平表达,诱导滑膜细胞凋亡,并改善DBA/1小鼠的胶原诱导性关节炎。Fas配体病毒还抑制胶原特异性T细胞产生干扰素-γ。Fas免疫球蛋白融合蛋白与Fas配体病毒共同给药可阻止这些效应,证明了Fas配体病毒的特异性。因此,在炎症部位进行FasL基因转移可有效改善自身免疫性疾病。