Holmberg Carina I, Staniszewski Kristine E, Mensah Kwame N, Matouschek Andreas, Morimoto Richard I
Department of Biochemistry, Molecular Biology and Cell Biology, Rice Institute for Biomedical Research, Robert H Lurie Comprehensive Cancer Center, Northwestern University, Evanston, IL 60208, USA.
EMBO J. 2004 Oct 27;23(21):4307-18. doi: 10.1038/sj.emboj.7600426. Epub 2004 Oct 7.
Accumulation of mutant proteins into misfolded species and aggregates is characteristic for diverse neurodegenerative diseases including the polyglutamine diseases. While several studies have suggested that polyglutamine protein aggregates impair the ubiquitin-proteasome system, the molecular mechanisms underlying the interaction between polyglutamine proteins and the proteasome have remained elusive. In this study, we use fluorescence live-cell imaging to demonstrate that the proteasome is sequestered irreversibly within aggregates of overexpressed N-terminal mutant Huntingtin fragment or simple polyglutamine expansion proteins. Moreover, by direct targeting of polyglutamine proteins for proteasomal degradation, we observe incomplete degradation of these substrates both in vitro and in vivo. Thus, our data reveal that intrinsic properties of the polyglutamine proteins prevent their efficient degradation and clearance. Additionally, fluorescence resonance energy transfer is detected between the proteasome and aggregated polyglutamine proteins indicative of a close and stable interaction. We propose that polyglutamine-containing proteins are kinetically trapped within proteasomes, which could explain their deleterious effects on cellular function over time.
突变蛋白积累形成错误折叠的物种和聚集体是包括多聚谷氨酰胺疾病在内的多种神经退行性疾病的特征。虽然多项研究表明多聚谷氨酰胺蛋白聚集体会损害泛素 - 蛋白酶体系统,但多聚谷氨酰胺蛋白与蛋白酶体之间相互作用的分子机制仍不清楚。在本研究中,我们使用荧光活细胞成像来证明蛋白酶体被不可逆地隔离在过表达的N端突变亨廷顿片段或简单多聚谷氨酰胺扩展蛋白的聚集体内。此外,通过将多聚谷氨酰胺蛋白直接靶向蛋白酶体降解,我们在体外和体内均观察到这些底物的不完全降解。因此,我们的数据表明多聚谷氨酰胺蛋白的内在特性阻止了它们的有效降解和清除。此外,在蛋白酶体和聚集的多聚谷氨酰胺蛋白之间检测到荧光共振能量转移,这表明存在紧密且稳定的相互作用。我们提出含多聚谷氨酰胺的蛋白在动力学上被困在蛋白酶体内,这可以解释它们随着时间推移对细胞功能的有害影响。