Reibarkh Mikhail, Malia Thomas J, Hopkins Brian T, Wagner Gerhard
Department of Biological Chemistry and Molecular Pharmacology, Harvard Medical School, Boston, MA 02115, USA.
J Biomol NMR. 2006 Sep;36(1):1-11. doi: 10.1007/s10858-006-9028-7. Epub 2006 Sep 9.
Interactions of proteins with small molecules or other macromolecules play key roles in many biological processes and in drug action, and NMR is an excellent tool for their structural characterization. Frequently, however, line broadening due to intermediate exchange completely eliminates the signals needed for measuring specific intermolecular NOEs. This limits the use of NMR for detailed structural studies in such kinetic situations. Here we show that an optimally chosen excess of ligand over protein can reduce the extent of line broadening for both the ligand and the protein. This makes observation of ligand resonances possible but reduces the size of the measurable NOEs due to the residual line broadening and the non-stoichiometric concentrations. Because the solubility of small molecule drug leads are often limited to high micromolar concentrations, protein concentrations are restricted to even lower values in the low micromolar range. At these non-stoichiometric concentrations and in the presence of significant residual line broadening, conventional NOESY experiments very often are not sensitive enough to observe intermolecular NOEs since the signals inverted by the NOESY preparation pulse sequence relax prior to significant NOE build up. Thus, we employ methods related to driven NOE spectroscopy to investigate protein-ligand interactions in the intermediate exchange regime. In this approach, individual protein resonances are selectively irradiated for up to five seconds to build up measurable NOEs at the ligand resonances. To enable saturation of individual protein resonances we prepare deuterated protein samples selectively protonated at a few sites so that the 1D (1)H spectrum of the protein is resolved well enough to permit irradiation of individual protein signals, which do not overlap with the ligand spectrum. This approach is suitable for measuring a sufficiently large number of protein-ligand NOEs that allow calculation of initial complex structures, suitable for structure-based optimization of primary drug leads obtained from high-throughput screening. The method was applied to measure individual intermolecular NOEs between the anti-apoptotic protein Bcl-xL at 25 microM and a "first generation" small-molecule ligand, for which the spectrum is entirely broadened at stoichiometric concentrations. This approach is general and can also be used to characterize protein-protein or protein-nucleic-acid complexes.
蛋白质与小分子或其他大分子之间的相互作用在许多生物过程和药物作用中起着关键作用,而核磁共振(NMR)是对其进行结构表征的出色工具。然而,由于中间交换导致的谱线展宽常常会完全消除测量特定分子间核Overhauser效应(NOE)所需的信号。这限制了NMR在这种动力学情况下用于详细结构研究的应用。在此我们表明,配体相对于蛋白质的最佳过量选择可以减少配体和蛋白质两者的谱线展宽程度。这使得观察配体共振成为可能,但由于残留的谱线展宽和非化学计量浓度,可测量的NOE大小会减小。由于小分子药物先导物的溶解度通常限制在高微摩尔浓度,蛋白质浓度在低微摩尔范围内甚至更低。在这些非化学计量浓度以及存在显著残留谱线展宽的情况下,传统的核Overhauser增强光谱(NOESY)实验往往不够灵敏,无法观察到分子间NOE,因为由NOESY制备脉冲序列反转的信号在显著的NOE积累之前就已经弛豫了。因此,我们采用与驱动NOE光谱相关的方法来研究中间交换区域的蛋白质 - 配体相互作用。在这种方法中,对单个蛋白质共振进行长达五秒的选择性照射,以在配体共振处积累可测量的NOE。为了使单个蛋白质共振饱和,我们制备在几个位点选择性质子化的氘代蛋白质样品,以便蛋白质的一维氢谱分辨率足够好,允许照射不与配体谱重叠的单个蛋白质信号。这种方法适用于测量足够数量的蛋白质 - 配体NOE,从而能够计算初始复合物结构,适用于对从高通量筛选获得的主要药物先导物进行基于结构的优化。该方法被应用于测量25微摩尔浓度下抗凋亡蛋白Bcl - xL与“第一代”小分子配体之间的单个分子间NOE,对于该配体,在化学计量浓度下其光谱完全展宽。这种方法具有通用性,也可用于表征蛋白质 - 蛋白质或蛋白质 - 核酸复合物。