Doronin Konstantin, Shashkova Elena V, May Shannon M, Hofherr Sean E, Barry Michael A
Division of Infectious Diseases, Department of Internal Medicine, Mayo Clinic, Rochester, MN 55902, USA.
Hum Gene Ther. 2009 Sep;20(9):975-88. doi: 10.1089/hum.2009.028.
Oncolytic adenoviruses are anticancer agents that replicate within tumors and spread to uninfected tumor cells, amplifying the anticancer effect of initial transduction. We tested whether coating the viral particle with polyethylene glycol (PEG) could reduce transduction of hepatocytes and hepatotoxicity after systemic (intravenous) administration of oncolytic adenovirus serotype 5 (Ad5). Conjugating Ad5 with high molecular weight 20-kDa PEG but not with 5-kDa PEG reduced hepatocyte transduction and hepatotoxicity after intravenous injection. PEGylation with 20-kDa PEG was as efficient at detargeting adenovirus from Kupffer cells and hepatocytes as virus predosing and warfarin. Bioluminescence imaging of virus distribution in two xenograft tumor models in nude mice demonstrated that PEGylation with 20-kDa PEG reduced liver infection 19- to 90-fold. Tumor transduction levels were similar for vectors PEGylated with 20-kDa PEG and unPEGylated vectors. Anticancer efficacy after a single intravenous injection was retained at the level of unmodified vector in large established prostate carcinoma xenografts, resulting in complete elimination of tumors in all animals and long-term tumor-free survival. Anticancer efficacy after a single intravenous injection was increased in large established hepatocellular carcinoma xenografts, resulting in significant prolongation of survival as compared with unmodified vector. The increase in efficacy was comparable to that obtained with predosing and warfarin pretreatment, significantly extending the median of survival. Shielding adenovirus with 20-kDa PEG may be a useful approach to improve the therapeutic window of oncolytic adenovirus after systemic delivery to primary and metastatic tumor sites.
溶瘤腺病毒是一种抗癌药物,可在肿瘤内复制并扩散至未感染的肿瘤细胞,从而增强初始转导的抗癌效果。我们测试了用聚乙二醇(PEG)包被病毒颗粒是否能减少溶瘤5型腺病毒(Ad5)全身(静脉)给药后对肝细胞的转导及肝毒性。将Ad5与高分子量20 kDa的PEG而非5 kDa的PEG偶联,可降低静脉注射后的肝细胞转导及肝毒性。用20 kDa的PEG进行聚乙二醇化在使腺病毒从库普弗细胞和肝细胞脱靶方面与病毒预给药及华法林一样有效。在裸鼠的两种异种移植肿瘤模型中对病毒分布进行的生物发光成像显示,用20 kDa的PEG进行聚乙二醇化可使肝脏感染减少19至90倍。用20 kDa的PEG聚乙二醇化的载体与未聚乙二醇化的载体的肿瘤转导水平相似。在大型已建立的前列腺癌异种移植瘤中,单次静脉注射后的抗癌疗效保持在未修饰载体的水平,导致所有动物的肿瘤完全消除并实现长期无瘤存活。在大型已建立的肝细胞癌异种移植瘤中,单次静脉注射后的抗癌疗效增强,与未修饰载体相比,生存期显著延长。疗效的提高与预给药及华法林预处理相当,显著延长了生存期的中位数。用20 kDa的PEG屏蔽腺病毒可能是一种有用的方法,可改善溶瘤腺病毒全身递送至原发性和转移性肿瘤部位后的治疗窗口。