Vision 1 year after gene therapy for Leber's congenital amaurosis.
作者信息
Cideciyan Artur V, Hauswirth William W, Aleman Tomas S, Kaushal Shalesh, Schwartz Sharon B, Boye Sanford L, Windsor Elizabeth A M, Conlon Thomas J, Sumaroka Alexander, Roman Alejandro J, Byrne Barry J, Jacobson Samuel G
出版信息
N Engl J Med. 2009 Aug 13;361(7):725-7. doi: 10.1056/NEJMc0903652.
Abstract
摘要
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