Gladstone Institute of Neurological Disease, Taube-Koret Center for Huntington's Disease Research, Consortium for Fronto-temporal Dementia Research, and Department of Neurology, University of California, San Francisco, California, USA.
Nat Med. 2010 Nov;16(11):1227-32. doi: 10.1038/nm.2222. Epub 2010 Sep 21.
Neurodegenerative diseases are the sixth leading cause of death in the US. The market for disease-modifying drugs is enormous, but no drug exists. Academic scientists are increasingly pursuing the discovery and development of therapeutics. Their progress could potentially reduce the risk of failure sufficiently to warrant greater industry investment and movement of leads into clinical trials. Here we consider the many obstacles to the development of therapeutics for neurodegenerative disease within academia, with a special focus on organizational issues.
神经退行性疾病是美国第六大致死原因。具有疾病修饰作用的药物市场巨大,但目前尚无此类药物。学术科学家越来越多地致力于治疗方法的发现和开发。他们的进展可能会降低失败的风险,从而足以吸引更多的行业投资,并将先导化合物推进临床试验。在这里,我们考虑了学术界中神经退行性疾病治疗方法开发所面临的许多障碍,特别关注组织问题。