Department of Chemical and Biological Engineering, University of Wisconsin, Madison, 1415 Engineering Drive, Madison, WI 53706, USA.
J Mol Biol. 2011 Sep 23;412(3):505-19. doi: 10.1016/j.jmb.2011.07.003. Epub 2011 Jul 29.
Abnormally expanded polyglutamine domains are associated with at least nine neurodegenerative diseases, including Huntington's disease. Expansion of the glutamine region facilitates aggregation of the impacted protein, and aggregation has been linked to neurotoxicity. Studies of synthetic peptides have contributed substantially to our understanding of the mechanism of aggregation because the underlying biophysics of polyglutamine-mediated association can be probed independent of their context within a larger protein. In this report, interrupting residues were inserted into polyglutamine peptides (Q20), and the impact on conformational and aggregation properties was examined. A peptide with two alanine residues formed laterally aligned fibrillar aggregates that were similar to the uninterrupted Q20 peptide. Insertion of two proline residues resulted in soluble, nonfibrillar aggregates, which did not mature into insoluble aggregates. In contrast, insertion of a β-turn template (D)PG rapidly accelerated aggregation and resulted in a fibrillar aggregate morphology with little lateral alignment between fibrils. These results are interpreted to indicate that (a) long-range nonspecific interactions lead to the formation of soluble oligomers, while maturation of oligomers into fibrils requires conformational conversion and (b) that soluble oligomers dynamically interact with each other, while insoluble aggregates are relatively inert. Kinetic analysis revealed that the increase in aggregation caused by the (D)PG insert is inconsistent with the nucleation-elongation mechanism of aggregation featuring a monomeric β-sheet nucleus. Rather, the data support a mechanism of polyglutamine aggregation by which monomers associate into soluble oligomers, which then undergo slow structural rearrangement to form sedimentable aggregates.
异常扩展的多聚谷氨酰胺结构域与至少九种神经退行性疾病有关,包括亨廷顿病。谷氨酰胺区域的扩展促进了受影响蛋白质的聚集,而聚集与神经毒性有关。对合成肽的研究极大地促进了我们对聚集机制的理解,因为可以在不考虑其在更大蛋白质中的上下文的情况下,探测多聚谷氨酰胺介导的关联的基础生物物理学。在本报告中,插入了中断残基到多聚谷氨酰胺肽(Q20)中,并检查了对构象和聚集特性的影响。具有两个丙氨酸残基的肽形成侧向对齐的纤维状聚集体,类似于未中断的 Q20 肽。插入两个脯氨酸残基导致可溶的、无纤维状的聚集体,这些聚集体不会成熟为不溶性聚集体。相比之下,插入 β-转角模板(D)PG 会迅速加速聚集,并导致纤维状聚集体形态,纤维之间几乎没有侧向对齐。这些结果表明:(a)长程非特异性相互作用导致可溶性寡聚物的形成,而寡聚物成熟为纤维需要构象转换;(b)可溶性寡聚物动态相互作用,而不溶性聚集体相对惰性。动力学分析表明,(D)PG 插入引起的聚集增加与具有单体β-片层核的聚合的成核-延伸机制不一致。相反,数据支持多聚谷氨酰胺聚集的机制,其中单体形成可溶性寡聚物,然后经历缓慢的结构重排形成可沉降的聚集体。