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International workshop on assessment of upper limb function in Duchenne Muscular Dystrophy: Rome, 15-16 February 2012.

作者信息

Mercuri Eugenio, McDonald Craig, Mayhew Anna, Florence Julaine, Mazzone Elena, Bianco Flaviana, Decostre Valerie, Servais Laurent, Ricotti Valeria, Goemans Nathalie, Vroom Elizabeth

机构信息

Department of Paediatric Neurology, Catholic University, Rome, Italy.

出版信息

Neuromuscul Disord. 2012 Nov;22(11):1025-8. doi: 10.1016/j.nmd.2012.06.006. Epub 2012 Jul 13.

DOI:10.1016/j.nmd.2012.06.006
PMID:22795657
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC3500683/
Abstract
摘要

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Upper limb strength and function changes during a one-year follow-up in non-ambulant patients with Duchenne Muscular Dystrophy: an observational multicenter trial.杜氏肌营养不良非行走患者一年随访期间上肢力量和功能变化:一项观察性多中心试验
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本文引用的文献

1
A critical review of functional assessment tools for upper limbs in Duchenne muscular dystrophy.杜氏肌营养不良症上肢功能评估工具的评价研究
Dev Med Child Neurol. 2012 Oct;54(10):879-85. doi: 10.1111/j.1469-8749.2012.04345.x. Epub 2012 Jun 19.
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Clinical outcome measures for trials in Duchenne muscular dystrophy: report from International Working Group meetings.杜氏肌营养不良症试验的临床结局指标:国际工作组会议报告
Clin Investig (Lond). 2011 Sep;1(9):1217-1235. doi: 10.4155/cli.11.113.
3
Assessing upper limb function in nonambulant SMA patients: development of a new module.评估非卧床型 SMA 患者的上肢功能:新模块的开发。
Neuromuscul Disord. 2011 Jun;21(6):406-12. doi: 10.1016/j.nmd.2011.02.014. Epub 2011 Mar 21.
4
Relationship between clinical outcome measures and parent proxy reports of health-related quality of life in ambulatory children with Duchenne muscular dystrophy.杜兴氏肌营养不良门诊患儿的临床结局指标与家长代理报告的健康相关生活质量之间的关系。
J Child Neurol. 2010 Sep;25(9):1130-44. doi: 10.1177/0883073810371509. Epub 2010 Jun 17.
5
Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France.迈向杜氏肌营养不良症(DMD)和脊髓性肌萎缩症(SMA)在TREAT-NMD项目中结局指标的统一;三场专家研讨会报告:TREAT-NMD/ENMC结局指标研讨会,2007年5月12日至13日,荷兰纳尔登;TREAT-NMD杜氏肌营养不良症实验性试验结局指标研讨会,2007年6月30日至7月1日,荷兰纳尔登;肌病学研究所与TREAT-NMD联合举办的神经肌肉疾病身体活动监测会议,2007年7月11日,法国巴黎。
Neuromuscul Disord. 2008 Nov;18(11):894-903. doi: 10.1016/j.nmd.2008.07.003. Epub 2008 Sep 24.
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A motor function measure for neuromuscular diseases. Construction and validation study.一种用于神经肌肉疾病的运动功能测量方法。构建与验证研究。
Neuromuscul Disord. 2005 Jul;15(7):463-70. doi: 10.1016/j.nmd.2005.03.004.
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Profiles of neuromuscular diseases. Duchenne muscular dystrophy.神经肌肉疾病概况。杜兴氏肌肉营养不良症。
Am J Phys Med Rehabil. 1995 Sep-Oct;74(5 Suppl):S70-92. doi: 10.1097/00002060-199509001-00003.
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Clinical trial in Duchenne dystrophy. I. The design of the protocol.杜氏肌营养不良症的临床试验。I. 方案设计
Muscle Nerve. 1981 May-Jun;4(3):186-97. doi: 10.1002/mus.880040304.
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An objective and standardized test of hand function.一项客观且标准化的手部功能测试。
Arch Phys Med Rehabil. 1969 Jun;50(6):311-9.