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Cost-effectiveness assessment of orphan drugs: a scientific and political conundrum.

作者信息

Simoens Steven, Picavet Eline, Dooms Marc, Cassiman David, Morel Thomas

出版信息

Appl Health Econ Health Policy. 2013 Feb;11(1):1-3. doi: 10.1007/s40258-012-0004-y.

DOI:10.1007/s40258-012-0004-y
PMID:23329382
Abstract
摘要

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[Authorization and reimbursement of orphan drugs in an international comparison].[国际比较中罕见病药物的授权与报销]
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Governance of conditional reimbursement practices in The Netherlands.荷兰有条件报销政策的管理
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How can the risk that orphan drugs present to budgets be managed better?如何更好地管理罕见病药物给预算带来的风险?
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[Orphan drugs: drugs for rare diseases].[孤儿药:用于罕见病的药物]
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Limits on use of health economic assessments for rare diseases.罕见病卫生经济评估的使用限制。
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