Department of Psychiatry, University of Minnesota, Minneapolis, MN 55454, USA.
Nutr Res. 2013 Nov;33(11):897-904. doi: 10.1016/j.nutres.2013.08.005. Epub 2013 Sep 16.
There are no biological treatments for fetal alcohol spectrum disorders (FASDs), lifelong conditions associated with physical anomalies, brain damage, and neurocognitive abnormalities. In preclinical studies, choline partially ameliorates memory and learning deficits from prenatal alcohol exposure. This phase I pilot study evaluated the feasibility, tolerability, and potential adverse effects of choline supplementation in children with FASD. We hypothesized that choline would be well tolerated with minimal adverse events. The study design was a double-blind, randomized, placebo-controlled trial. Participants included 20 children aged 2.5 to 4.9 years with prenatal alcohol exposure and FASD diagnoses. Participants were randomly assigned to 500 mg choline or placebo daily for 9 months (10 active, 10 placebo). Primary outcome measures included feasibility, tolerability, adverse effects, and serum choline levels. Seventeen participants completed the study. Compliance was 82% to 87%, as evidenced by parent-completed log sheets and dose counts. Periodic 24-hour dietary recalls showed no evidence of dietary confounding. Adverse events were minimal and were equivalent in the active and placebo arms with the exception of fishy body odor, which occurred only in the active group. There were no serious adverse events to research participants. This phase I pilot study demonstrates that choline supplementation at 500 mg/d for 9 months in children aged 2 to 5 years is feasible and has high tolerability. Further examination of the efficacy of choline supplementation in FASD is currently underway.
目前尚无治疗胎儿酒精谱系障碍(FASD)的生物学方法,FASD 是一种终身性疾病,会导致身体畸形、大脑损伤和神经认知异常。在临床前研究中,胆碱可部分改善产前酒精暴露引起的记忆和学习缺陷。本 I 期试点研究评估了胆碱补充剂在 FASD 儿童中的可行性、耐受性和潜在不良反应。我们假设胆碱的耐受性良好,仅有轻微不良反应。研究设计为双盲、随机、安慰剂对照试验。参与者包括 20 名年龄在 2.5 至 4.9 岁之间、有产前酒精暴露史和 FASD 诊断的儿童。参与者被随机分配至每天接受 500mg 胆碱或安慰剂治疗,共 9 个月(10 名接受活性药物治疗,10 名接受安慰剂治疗)。主要结局指标包括可行性、耐受性、不良反应和血清胆碱水平。17 名参与者完成了研究。根据家长填写的日志表和剂量计数,依从性为 82%至 87%。定期的 24 小时膳食回顾未发现饮食混杂的证据。不良反应较少,且在活性药物组和安慰剂组中相当,仅活性药物组出现鱼腥味体臭。研究参与者无严重不良事件。本 I 期试点研究表明,2 至 5 岁儿童每天补充 500mg 胆碱 9 个月是可行的,且具有较高的耐受性。目前正在进一步研究胆碱补充剂治疗 FASD 的疗效。